Hematologic Cancer after Gene Therapy for Cerebral Adrenoleukodystrophy
脑肾上腺脑白质营养不良基因治疗后的血液系统癌症
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa2405541
Duncan, Christine N; Bledsoe, Jacob R; Grzywacz, Bartosz; Beckman, Amy; Bonner, Melissa; Eichler, Florian S; Kühl, Jörn-Sven; Harris, Marian H; Slauson, Sarah; Colvin, Richard A; Prasad, Vinod K; Downey, Gerald F; Pierciey, Francis J; Kinney, Melissa A; Foos, Marianna; Lodaya, Ankit; Floro, Nicole; Parsons, Geoffrey; Dietz, Andrew C; Gupta, Ashish O; Orchard, Paul J; Thakar, Himal L; Williams, David A