Randomized phase 2 study of ACE-083, a muscle-promoting agent, in facioscapulohumeral muscular dystrophy
ACE-083(一种肌肉促进剂)治疗面肩肱型肌营养不良症的随机二期研究
期刊:Muscle & Nerve
影响因子:3.1
doi:10.1002/mus.27558
Statland, Jeffrey M; Campbell, Craig; Desai, Urvi; Karam, Chafic; Díaz-Manera, Jordi; Guptill, Jeffrey T; Korngut, Lawrence; Genge, Angela; Tawil, Rabi N; Elman, Lauren; Joyce, Nanette C; Wagner, Kathryn R; Manousakis, Georgios; Amato, Anthony A; Butterfield, Russell J; Shieh, Perry B; Wicklund, Matthew; Gamez, Josep; Bodkin, Cynthia; Pestronk, Alan; Weihl, Conrad C; Vilchez-Padilla, Juan J; Johnson, Nicholas E; Mathews, Katherine D; Miller, Barry; Leneus, Ashley; Fowler, Marcie; van de Rijn, Marc; Attie, Kenneth M