Targeted exon skipping to address "leaky" mutations in the dystrophin gene
利用靶向外显子跳跃技术解决肌营养不良蛋白基因中的“渗漏”突变
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1038/mtna.2012.40
Fletcher, Sue; Adkin, Carl F; Meloni, Penny; Wong, Brenda; Muntoni, Francesco; Kole, Ryszard; Fragall, Clayton; Greer, Kane; Johnsen, Russell; Wilton, Steve D
