日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Elucidating brain transport pathways and cell type-dependent gene silencing of a durable lipid-siRNA conjugate administered into cerebrospinal fluid.

阐明脑脊液中注入的持久性脂质-siRNA缀合物的脑运输途径和细胞类型依赖性基因沉默

Sorets Alexander G, Schwensen Katrina R, Francini Nora, Kjar Andrew, Abdulrahman Adam M, Shostak Alena, Katdare Ketaki A, Schoch Kathleen M, Cowell Rebecca P, Park Joshua C, Ligocki Alexander P, Ford William T, Ventura-Antunes Lissa, Hoogenboezem Ella N, Prusky Alex, Castleberry Mark, Michell Danielle L, Fritsch Emma, Lyons Sarah M, Miller Timothy M, Vickers Kasey C, Schrag Matthew S, Duvall Craig L, Lippmann Ethan S

Covalent Polymer-RNA Conjugates for Potent Activation of the RIG-I Pathway

共价聚合物-RNA缀合物可有效激活RIG-I通路

Palmer, Christian R; Pastora, Lucinda E; Kimmel, Blaise R; Pagendarm, Hayden M; Kwiatkowski, Alexander J; Stone, Payton T; Arora, Karan; Francini, Nora; Fedorova, Olga; Pyle, Anna M; Wilson, John T

Induction of Triple-Negative Breast Cancer Cell Death and Chemosensitivity Using mTORC2-Directed RNAi Nanomedicine.

利用 mTORC2 靶向 RNAi 纳米药物诱导三阴性乳腺癌细胞死亡和化疗敏感性

Patel Shrusti S, Cook Rebecca S, Lo Justin H, Cherry Fiona K, Hoogenboezem Ella N, Yu Fang, Francini Nora, Cassidy Nina T, McCune Joshua T, Gbur Eva F, Messier Lisa, Dean Thomas A, Wilson Kalin L, Brantley-Sieders Dana M, Duvall Craig L

Evaluating the effects of aging on biodistribution and gene silencing activity of lipid-siRNA conjugates delivered into cerebrospinal fluid

评估衰老对递送至脑脊液中的脂质-siRNA缀合物的生物分布和基因沉默活性的影响

Ligocki, Alexander P; Sorets, Alexander G; Abdulrahman, Adam M; Francini, Nora; Park, Joshua C; Lee, Ju Ha; Ford, William T; Lyons, Sarah M; Fritsch, Emma L; Lamantia, Zachary E; Christov, Plamen P; Duvall, Craig L; Lippmann, Ethan S

Intravenous lipid-siRNA conjugate mediates gene silencing at the blood-brain barrier and blood-CSF barrier.

静脉注射脂质-siRNA偶联物可介导血脑屏障和血脑脊液屏障处的基因沉默

Sorets Alexander G, Schwensen Katrina R, Francini Nora, Kjar Andrew, Lyons Sarah, Park Joshua C, Palmer Dillon, Abdulrahman Adam M, Cowell Rebecca P, Katdare Ketaki A, Hoogenboezem Ella N, Wang Angela, Dani Neil, Duvall Craig L, Lippmann Ethan S

Engineering approaches for RNA-based and cell-based osteoarthritis therapies

基于RNA和细胞的骨关节炎治疗的工程方法

DeJulius, Carlisle R; Walton, Bonnie L; Colazo, Juan M; d'Arcy, Richard; Francini, Nora; Brunger, Jonathan M; Duvall, Craig L

Synthesis and characterization of chloroquine-modified albumin-binding siRNA-lipid conjugates for improved intracellular delivery and gene silencing in cancer cells

合成和表征氯喹修饰的白蛋白结合siRNA-脂质缀合物,以改善癌细胞内的递送和基因沉默效果

Lo, Justin H; Gbur, Eva F; Francini, Nora; Ma, Jinqi; Sorets, Alexander G; Fletcher, R Brock; Yu, Fang; D'Arcy, Richard; Oltman, Connor G; Uddin, Md Jashim; Duvall, Craig L

Core polymer optimization of ternary siRNA nanoparticles enhances in vivo safety, pharmacokinetics, and tumor gene silencing

三元siRNA纳米粒子的核心聚合物优化可增强体内安全性、药代动力学和肿瘤基因沉默能力

Patel, Shrusti S; Hoogenboezem, Ella N; Yu, Fang; DeJulius, Carlisle R; Fletcher, R Brock; Sorets, Alex G; Cherry, Fiona K; Lo, Justin H; Bezold, Mariah G; Francini, Nora; d'Arcy, Richard; Brasuell, Jordan E; Cook, Rebecca S; Duvall, Craig L

Albumin-binding RNAi Conjugate for Carrier Free Treatment of Arthritis

用于无载体治疗关节炎的白蛋白结合RNAi偶联物

Colazo, Juan M; Hoogenboezem, Ella N; Keech, Megan C; Francini, Nora; Shah, Veeraj; Yu, Fang; Lo, Justin H; Sorets, Alexander G; McCune, Joshua T; Cho, Hongsik; DeJulius, Carlisle R; Michell, Danielle L; Maerz, Tristan; Vickers, Kacey C; Gibson-Corley, Katherine N; Hasty, Karen A; Crofford, Leslie; Cook, Rebecca S; Duvall, Craig L

A Reactive Oxygen Species-Scavenging 'Stealth' Polymer, Poly(thioglycidyl glycerol), Outperforms Poly(ethylene glycol) in Protein Conjugates and Nanocarriers and Enhances Protein Stability to Environmental and Biological Stressors

活性氧清除“隐形”聚合物聚(硫代缩水甘油)在蛋白质偶联物和纳米载体中性能优于聚(乙二醇),并能增强蛋白质对环境和生物胁迫的稳定性。

d'Arcy, Richard; El Mohtadi, Farah; Francini, Nora; DeJulius, Carlisle R; Back, Hyunmoon; Gennari, Arianna; Geven, Mike; Lopez-Cavestany, Maria; Turhan, Zulfiye Yesim; Yu, Fang; Lee, Jong Bong; King, Michael R; Kagan, Leonid; Duvall, Craig L; Tirelli, Nicola