日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

ZFTA-RELA ependymomas make itaconate to epigenetically drive fusion expression

ZFTA-RELA室管膜瘤通过表观遗传驱动融合表达,产生衣康酸。

Natarajan, Siva Kumar; Lum, Joanna; Skeans, James Haggerty; Nenwani, Minal; Eyunni, Sanjana; Mota, Mateus; Bayliss, Jill M; Deogharkar, Akash; Hamanishi, Erin Taya; Pun, Matthew; Sweha, Stefan R; Hoffman, Simon; Young, Eleanor; Zhang, Qiuyang; Mehta, Rijul; Animasahun, Olamide; Narayanan, Pranav; Sunil, Sushanth; Parolia, Abhijit; Sajjakulnukit, Peter; Panwalkar, Pooja; Doherty, Robert; Clausen, Madison; Dang, Derek; Hawes, Debra; Yang, Fusheng; Santi, Mariarita; Judkins, Alexander R; Wilson, Yelena; Vigil, Thomas; Franson, Andrea; Mortensen, Richard M; Ozawa, Tatsuya; Griesinger, Andrea; Holland, Eric C; Foreman, Nicholas K; Michealraj, Kulandaimanuvel Antony; Agnihotri, Sameer; Taylor, Michael; Gilbertson, Richard J; Koschmann, Carl; Chinnaiyan, Arul M; Lyssiotis, Costas A; Nagrath, Deepak; Venneti, Sriram

AI-powered segmentation and prognosis with missing MRI in pediatric brain tumors

利用人工智能技术对缺失MRI图像的儿童脑肿瘤进行分割和预后分析

Chrysochoou, Dimosthenis; Gandhi, Deep B; Adib, Sahand; Familiar, Ariana M; Vunnava, Bhavyasri; Varshochi, Sanaz; Khalili, Neda; Khalili, Nastaran; Ware, Jeffrey B; Tu, Wenxin; Jain, Paarth; Anderson, Hannah; Haldar, Shuvanjan; Storm, Phillip B; Franson, Andrea; Prados, Michael; Kline, Cassie; Mueller, Sabine; Resnick, Adam; Vossough, Arastoo; Davatzikos, Christos; Nabavizadeh, Ali; Kazerooni, Anahita Fathi

First-in-child phase I trial of p-STAT3 inhibitor WP1066 in pediatric brain tumor patients

首个针对儿童的p-STAT3抑制剂WP1066在儿童脑肿瘤患者中的I期临床试验

Castellino, Robert C; Mumme, Hope; Franson, Andrea; Yu, Bing; Robinson, Hope; Dhodapkar, Kavita; Aguilera, Dolly; Schniederjan, Matthew; Keesari, Rohali; He, Zhulin; Bhasin, Manoj; Priebe, Waldemar; Heimberger, Amy B; MacDonald, Tobey J

Local ancestry modulates gene expression: shifting our understanding of genetic regulation and disease association within and across populations

局部祖先特征调节基因表达:改变我们对群体内部和群体间基因调控和疾病关联的理解

Chen, Hung-Hsin; Cai, Yanwei; Graff, MariaElisa; Zhu, Wanying; Petty, Lauren E; Highland, Heather M; Roshani, Rashedah; Polikowsky, Hannah G; Lorenz, Anna S; Frankel, Elizabeth; Landman, Joshua M; Anwar, Mohammad Y; Franson, Elyn E; Haessler, Jeffrey; Avery, Christy L; Young, Kristin L; Fernandez-Rhodes, Lindsay; Reiner, Alexander P; Peters, Ulrike; Gordon-Larsen, Penny; Gamazon, Eric R; Pereira, Alexandre C; Kooperberg, Charles; Huff, Chad D; Fisher-Hoch, Susan P; McCormick, Joseph B; North, Kari E; Below, Jennifer E

Author Correction: The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

作者更正:II型RAF抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:FIREFLY-1 II期试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

Isocitrate dehydrogenase 1 primes group-3 medulloblastomas for cuproptosis

异柠檬酸脱氢酶 1 启动 3 组髓母细胞瘤发生铜凋亡

Derek Dang ,Akash Deogharkar ,John McKolay ,Kyle S Smith ,Pooja Panwalkar ,Simon Hoffman ,Wentao Tian ,Sunjong Ji ,Ana P Azambuja ,Siva Kumar Natarajan ,Joanna Lum ,Jill Bayliss ,Katie Manzeck ,Stefan R Sweha ,Erin Hamanishi ,Matthew Pun ,Diya Patel ,Sagar Rau ,Olamide Animasahun ,Abhinav Achreja ,Martin P Ogrodzinski ,Jutta Diessl ,Jennifer Cotter ,Debra Hawes ,Fusheng Yang ,Robert Doherty ,Andrea T Franson ,Allison R Hanaford ,Charles G Eberhart ,Eric H Raabe ,Brent A Orr ,Robert J Wechsler-Reya ,Brandon Chen ,Costas A Lyssiotis ,Yatrik M Shah ,Sophia Y Lunt ,Ruma Banerjee ,Alexander R Judkins ,John R Prensner ,Carl Koschmann ,Sebastian M Waszak ,Deepak Nagrath ,Marcos Simoes-Costa ,Paul A Northcott ,Sriram Venneti

ReNeu: A Pivotal, Phase IIb Trial of Mirdametinib in Adults and Children With Symptomatic Neurofibromatosis Type 1-Associated Plexiform Neurofibroma

ReNeu:一项针对有症状的1型神经纤维瘤病相关丛状神经纤维瘤成人和儿童的米达替尼关键性IIb期试验

Moertel, Christopher L; Hirbe, Angela C; Shuhaiber, Hans H; Bielamowicz, Kevin; Sidhu, Alpa; Viskochil, David; Weber, Michael D; Lokku, Armend; Smith, L Mary; Foreman, Nicholas K; Hajjar, Fouad M; McNall-Knapp, Rene Y; Weintraub, Lauren; Antony, Reuben; Franson, Andrea T; Meade, Julia; Schiff, David; Walbert, Tobias; Ambady, Prakash; Bota, Daniela A; Campen, Cynthia J; Kaur, Gurcharanjeet; Klesse, Laura J; Maraka, Stefania; Moots, Paul L; Nevel, Kathryn; Bornhorst, Miriam; Aguilar-Bonilla, Ana; Chagnon, Sarah; Dalvi, Nagma; Gupta, Punita; Khatib, Ziad; Metrock, Laura K; Nghiemphu, P Leia; Roberts, Ryan D; Robison, Nathan J; Sadighi, Zsila; Stapleton, Stacie; Babovic-Vuksanovic, Dusica; Gershon, Timothy R

Correction: Clinical Efficacy of ONC201 in H3K27M-Mutant Diffuse Midline Gliomas Is Driven by Disruption of Integrated Metabolic and Epigenetic Pathways

更正:ONC201治疗H3K27M突变型弥漫性中线胶质瘤的临床疗效是由整合代谢和表观遗传通路紊乱驱动的

Venneti, Sriram; Kawakibi, Abed Rahman; Ji, Sunjong; Waszak, Sebastian M; Sweha, Stefan R; Mota, Mateus; Pun, Matthew; Deogharkar, Akash; Chung, Chan; Tarapore, Rohinton S; Ramage, Samuel; Chi, Andrew; Wen, Patrick Y; Arrillaga-Romany, Isabel; Batchelor, Tracy T; Butowski, Nicholas A; Sumrall, Ashley; Shonka, Nicole; Harrison, Rebecca A; de Groot, John; Mehta, Minesh; Hall, Matthew D; Daghistani, Doured; Cloughesy, Timothy F; Ellingson, Benjamin M; Beccaria, Kevin; Varlet, Pascale; Kim, Michelle M; Umemura, Yoshie; Garton, Hugh; Franson, Andrea; Schwartz, Jonathan; Jain, Rajan; Kachman, Maureen; Baum, Heidi; Burant, Charles F; Mottl, Sophie L; Cartaxo, Rodrigo T; John, Vishal; Messinger, Dana; Qin, Tingting; Peterson, Erik; Sajjakulnukit, Peter; Ravi, Karthik; Waugh, Alyssa; Walling, Dustin; Ding, Yujie; Xia, Ziyun; Schwendeman, Anna; Hawes, Debra; Yang, Fusheng; Judkins, Alexander R; Wahl, Daniel; Lyssiotis, Costas A; Nava, Daniel de la; Alonso, Marta M; Eze, Augustine; Spitzer, Jasper; Schmidt, Susanne V; Duchatel, Ryan J; Dun, Matthew D; Cain, Jason E; Jiang, Li; Stopka, Sylwia A; Baquer, Gerard; Regan, Michael S; Filbin, Mariella G; Agar, Nathalie Y R; Zhao, Lili; Kumar-Sinha, Chandan; Mody, Rajen; Chinnaiyan, Arul; Kurokawa, Ryo; Pratt, Drew; Yadav, Viveka N; Grill, Jacques; Kline, Cassie; Mueller, Sabine; Resnick, Adam; Nazarian, Javad; Allen, Joshua E; Odia, Yazmin; Gardner, Sharon L; Koschmann, Carl

Radiographic and visual response to the type II RAF inhibitor tovorafenib in children with relapsed/refractory optic pathway glioma in the FIREFLY-1 trial

FIREFLY-1试验中,复发/难治性视路胶质瘤患儿对II型RAF抑制剂托沃拉非尼的放射学和视觉反应

Nysom, Karsten; Kilburn, Lindsay B; Leary, Sarah E S; Landi, Daniel B; de Vos-Kerkhof, Evelien; Perreault, Sébastien; Witt, Olaf; Ziegler, David S; Hernáiz Driever, Pablo; Franson, Andrea T; Baxter, Patricia A; Whipple, Nicholas S; Kline, Cassie; Segal, Devorah; Jabado, Nada; Bailey, Simon; McCowage, Geoffrey; Hansford, Jordan R; Khuong-Quang, Dong-Anh; Gottardo, Nicholas G; Hassall, Timothy; Han, Jung Woo; Yalon Oren, Michal; Chi, Susan N; Qiu, Jiaheng; Da Costa, Daniel; Govinda Raju, Sandya; Manley, Peter; Hargrave, Darren

Single-molecule systems for the detection and monitoring of plasma-circulating nucleosomes and oncoproteins in diffuse midline glioma

用于检测和监测弥漫性中线胶质瘤中血浆循环核小体和癌蛋白的单分子系统

Nir Erez, Noa Furth, Vadim Fedyuk, Jack Wadden, Rayan Aittaleb, Tiffany Adam, Kallen Schwark, Michael Niculcea, Madeline Miclea, Rajen Mody, Andrea Franson, Hemant A Parmar, Mohannad Ibrahim, Benison Lau, Augustine Eze, Niku Nourmohammadi, Iris Fried, Javad Nazarian, Guy Ron, Sriram Venneti, Carl Ko