In vivo prime editing rescues photoreceptor degeneration in nonsense mutant retinitis pigmentosa.
体内基因编辑可挽救无义突变视网膜色素变性中的感光细胞退化
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-57628-6
Fu Yidian, He Xiaoyu, Ma Liang, Gao Xin D, Liu Pengpeng, Shi Hanhan, Chai Peiwei, Ge Shengfang, Jia Renbing, Liu David R, Fan Xianqun, Yang Zhi