日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Charting the translational pathway: ISSCR best practices for the development of PSC-derived therapies

规划转化路径:ISSCR关于PSC衍生疗法开发的最佳实践

Barry, Jacqueline; Abranches, Elsa; Baptista, Ricardo P; Barry, Chris; Brandsten, Catharina; Bruce, Kevin; Carpenter, Melissa K; Cavagnaro, Joy; Collins, Lila; Csaszar, Elizabeth; Dashnau, Jennifer; de Villa, Denise; Fynes, Kate; Gabaldo, Michela; Hao, Jie; Harel-Adar, Tamar; Hei, Derek; Henchcliffe, Claire; Hidalgo-Simon, Ana; Hollands, Jennifer; Hursh, Deborah; Jackman, Shawna; Kelly, Kilian; Kim, Jung-Hyun; Kim, Hyunyoung; Kino-Oka, Masahiro; Lakshmipathy, Uma; Lamb, Tyler; Lazic, Stanley E; Loring, Jeanne F; Ludwig, Tenneille E; Mariappan, Indumathi; Monville, Christelle; Mountford, Joanne C; Nagy, Andras; Okano, Hideyuki; Pellegrini, Graziella; Persson, Annelie; Prutton, Kendra; Rasko, John E J; Sareen, Dhruv; Sato, Yoji; Shnaiderman, Anat; Stacey, Glyn; Svendsen, Clive N; Tomishima, Mark; Trounson, Alan; Viswanathan, Sowmya; Wang, Shuyan; Wydenbach, Kirsty; Zhang, Alex; Zylberberg, Claudia; Mosher, Jack T; Bharti, Kapil

User-Centered Design of Trauma Systems Solutions for Retriage of Patients With Injury: Mixed Methods Study

以用户为中心的创伤系统解决方案设计:用于伤员分诊的混合方法研究

Slocum, John Dwight; Jelke, David; Mai, Qixuan; Johnson, Julie K; Nguyen, My L T; Cong, Lixuan; Chandrasekaran, Adithya; Holl, Jane L; Moklyak, Yuriy; Mis, Justin; Gabaldo, Molly; Adams, James G; Brigode, William M; Voights, Mary Beth; Andersen, Rebecca; Gilbert, Tamuriat; Siparsky, Nicole; Proust, Arthur; Stey, Anne M; Berry, Andrew B L

Advanced Practice Public Health Nursing (APHN) in the U.S.: Roles and Education

美国高级公共卫生护理实践(APHN):角色与教育

Swider, Susan M; Harpin, Scott; Balint, Katherine; Edwards, Lori; Eustace, Rosemary; Gabaldo, Molly; Glauberman, Gary; Haushalter, Alisa; Holt, Mikaila; Jones, Krista; Mehringer, Angela; Novacek, Lindsay; Pearce, Melanie; Prentice, Ashley

Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency

逆转录病毒基因疗法治疗腺苷脱氨酶缺乏症的长期和真实世界安全性和有效性

Migliavacca, Maddalena; Barzaghi, Federica; Fossati, Claudia; Rancoita, Paola M V; Gabaldo, Michela; Dionisio, Francesca; Giannelli, Stefania; Salerio, Federica Andrea; Ferrua, Francesca; Tucci, Francesca; Calbi, Valeria; Gallo, Vera; Recupero, Salvatore; Consiglieri, Giulia; Pajno, Roberta; Sambuco, Maria; Priolo, Alessio; Ferri, Chiara; Garella, Vittoria; Monti, Ilaria; Silvani, Paolo; Darin, Silvia; Casiraghi, Miriam; Corti, Ambra; Zancan, Stefano; Levi, Margherita; Cesana, Daniela; Carlucci, Filippo; Pituch-Noworolska, Anna; AbdElaziz, Dalia; Baumann, Ulrich; Finocchi, Andrea; Cancrini, Caterina; Ladogana, Saverio; Meinhardt, Andrea; Meyts, Isabelle; Montin, Davide; Notarangelo, Lucia Dora; Porta, Fulvio; Pasquet, Marlène; Speckmann, Carsten; Stepensky, Polina; Tommasini, Alberto; Rabusin, Marco; Karakas, Zeynep; Galicchio, Miguel; Leonardi, Lucia; Duse, Marzia; Guner, Sukru Nail; Di Serio, Clelia; Ciceri, Fabio; Bernardo, Maria Ester; Aiuti, Alessandro; Cicalese, Maria Pia

INTERVENTIONAL TRAPS IN ECTATIC CORONARY ARTERIES: A CASE REPORT

介入性血管夹闭术治疗扩张性冠状动脉:病例报告

Gabaldo, Krešimir; Knežević Praveček, Marijana; Vučić, Domagoj; Mišković, Domagoj; Bitunjac, Ivan; Dunđer, Ivica; Vujeva, Božo; Miškić, Blaženka; Cvitkušić Lukenda, Katica

How to START? Four pillars to optimally begin your orphan drug development

如何起步?四大支柱助您高效启动孤儿药研发

Jonker, Anneliene Hechtelt; Batista, Liliana; Gabaldo, Michela; Hivert, Virginie; Ardigo, Diego

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

慢病毒造血干细胞基因疗法治疗早发性异染性脑白质营养不良:一项非随机、开放标签的1/2期临床试验的长期结果及扩大用药范围

Fumagalli, Francesca; Calbi, Valeria; Natali Sora, Maria Grazia; Sessa, Maria; Baldoli, Cristina; Rancoita, Paola Maria V; Ciotti, Francesca; Sarzana, Marina; Fraschini, Maddalena; Zambon, Alberto Andrea; Acquati, Serena; Redaelli, Daniela; Attanasio, Vanessa; Miglietta, Simona; De Mattia, Fabiola; Barzaghi, Federica; Ferrua, Francesca; Migliavacca, Maddalena; Tucci, Francesca; Gallo, Vera; Del Carro, Ubaldo; Canale, Sabrina; Spiga, Ivana; Lorioli, Laura; Recupero, Salvatore; Fratini, Elena Sophia; Morena, Francesco; Silvani, Paolo; Calvi, Maria Rosa; Facchini, Marcella; Locatelli, Sara; Corti, Ambra; Zancan, Stefano; Antonioli, Gigliola; Farinelli, Giada; Gabaldo, Michela; Garcia-Segovia, Jesus; Schwab, Laetitia C; Downey, Gerald F; Filippi, Massimo; Cicalese, Maria Pia; Martino, Sabata; Di Serio, Clelia; Ciceri, Fabio; Bernardo, Maria Ester; Naldini, Luigi; Biffi, Alessandra; Aiuti, Alessandro

The EHA Research Roadmap: Hematopoietic Stem Cell Gene Therapy

EHA研究路线图:造血干细胞基因治疗

Naldini, Luigi; Cicalese, Maria Pia; Bernardo, Maria Ester; Gentner, Bernhard; Gabaldo, Michela; Ferrari, Giuliana; Aiuti, Alessandro

Quality of Life and Anorectal Malformations: A Single-Center Experience

生活质量与肛门直肠畸形:单中心经验

Scirè, Gabriella; Gabaldo, Riccardo; Dando, Ilaria; Camoglio, Francesco S; Zampieri, Nicola

Diagnostic complexity of rifampicin-induced coagulopathy in a patient with spontaneous muscle bleeding: A case report

利福平诱发凝血功能障碍合并自发性肌肉出血患者的诊断复杂性:病例报告

Vučić, Domagoj; Cvitkušić-Lukenda, Katica; Dunđer, Ivica; Gabaldo, Krešimir; Knežević-Praveček, Marijana; Miškić, Blaženka