Efficient modification of CCR5 in primary human hematopoietic cells using a megaTAL nuclease and AAV donor template
使用 megaTAL 核酸酶和 AAV 供体模板对原代人类造血细胞中的 CCR5 进行有效修饰
期刊:Science Translational Medicine
影响因子:15.8
doi:10.1126/scitranslmed.aac5530
Blythe D Sather, Guillermo S Romano Ibarra, Karen Sommer, Gabrielle Curinga, Malika Hale, Iram F Khan, Swati Singh, Yumei Song, Kamila Gwiazda, Jaya Sahni, Jordan Jarjour, Alexander Astrakhan, Thor A Wagner, Andrew M Scharenberg, David J Rawlings