Zinc finger nuclease-mediated gene editing in hematopoietic stem cells results in reactivation of fetal hemoglobin in sickle cell disease
锌指核酸酶介导的造血干细胞基因编辑可导致镰状细胞病中胎儿血红蛋白的重新激活
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/s41598-024-74716-7
Samuel Lessard #,Pauline Rimmelé #,Hui Ling,Kevin Moran,Benjamin Vieira,Yi-Dong Lin,Gaurav Manohar Rajani,Vu Hong,Andreas Reik,Richard Boismenu,Ben Hsu,Michael Chen,Bettina M Cockroft,Naoya Uchida,John Tisdale,Asif Alavi,Lakshmanan Krishnamurti,Mehrdad Abedi,Isobelle Galeon,David Reiner,Lin Wang,Anne Ramezi,Pablo Rendo,Mark C Walters,Dana Levasseur,Robert Peters,Timothy Harris,Alexandra Hicks
