Efficacy of Switching Therapy From Alglucosidase Alfa to Avalglucosidase Alfa on Respiratory Function in Participants With Late-Onset Pompe Disease: A Post Hoc Analysis From the COMET Trial
在晚发型庞贝病患者中，从阿糖苷酶α换用阿伐糖苷酶α治疗对呼吸功能的影响：COMET试验的事后分析
期刊:JIMD Reports
影响因子:1.8
doi:10.1002/jmd2.70033
Kishnani, Priya S; Boentert, Matthias; Wenninger, Stephan; Berger, Kenneth I; Msihid, Jérôme; O'Callaghan, Lasair; Essadi-Addou, Rachida; Gallego, Victor; Rawat, Neeraj Singh; Huynh-Ba, Olivier; Diaz-Manera, Jordi
