Utilizing AAV-mediated LEAPER 2.0 for programmable RNA editing in non-human primates and nonsense mutation correction in humanized Hurler syndrome mice
利用AAV介导的LEAPER 2.0在非人灵长类动物中进行可编程RNA编辑，并在人源化Hurler综合征小鼠中进行无义突变校正
期刊:Genome Biology
影响因子:10.1
doi:10.1186/s13059-023-03086-6
Zongyi Yi # ,Yanxia Zhao # ,Zexuan Yi # ,Yongjian Zhang # ,Gangbin Tang ,Xiaoxue Zhang ,Huixian Tang ,Wei Zhang ,Ying Zhao ,Huayuan Xu ,Yuyang Nie ,Xueqing Sun ,Lijun Xing ,Lian Dai ,Pengfei Yuan ,Wensheng Wei
