日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Hematopoietic Stem-Cell Gene Therapy for Cystinosis

胱氨酸病的造血干细胞基因治疗

Barshop, Bruce A; Ball, Edward D; Benador, Nadine; Trauner, Doris; Phillips, Susan; Dohil, Ranjan; Afshari, Natalie A; Roy, Sohini; Campo Fernandes, Beatriz; Kohn, Donald; Shayan, Katayoon; Everett, John K; Bushman, Frederic D; Midgley, Julian; Liang, Hong; Sawyers, Anne; Gangoiti, Jon A; Panchal, Maulik; Ahmed, Imama; Cherqui, Stephanie

Use of an oversized AAV8 vector for CPS1 deficiency results in long-term survival and ammonia control.

使用超大的 AAV8 载体治疗 CPS1 缺陷可实现长期存活和氨控制

Diep Taryn, Zhou Wesley, Reyes Rachel E, Nitzahn Matthew, Day Isabel L, Makris Georgios, Lueptow Lindsay, Zhuravka Irina, Bakshi Stuti, Gangoiti Jon, Padaon Hyacinth, Li Yunfeng, Barshop Bruce A, Haberle Johannes, Lipshutz Gerald S

Metformin reverts aortic calcifications and elastin loss induced by an experimental metabolic syndrome

二甲双胍可逆转实验性代谢综合征引起的主动脉钙化和弹性蛋白丢失。

Streckwall, Lucas; Martini, Nancy; Sedlinsky, Claudia; Schurman, León; Gangoiti, María Virginia; McCarthy, Antonio Desmond

Phosphatidic Acid Stimulates Lung Cancer Cell Migration through Interaction with the LPA1 Receptor and Subsequent Activation of MAP Kinases and STAT3

磷脂酸通过与 LPA1 受体相互作用以及随后激活 MAP 激酶和 STAT3 来刺激肺癌细胞迁移

Ana Gomez-Larrauri, Patricia Gangoiti, Laura Camacho, Natalia Presa, Cesar Martin, Antonio Gomez-Muñoz

Outcomes of SARS-CoV-2-Positive Youths Tested in Emergency Departments: The Global PERN-COVID-19 Study

急诊科检测呈 SARS-CoV-2 阳性青少年的结局:全球 PERN-COVID-19 研究

Funk, Anna L; Florin, Todd A; Kuppermann, Nathan; Tancredi, Daniel J; Xie, Jianling; Kim, Kelly; Neuman, Mark I; Ambroggio, Lilliam; Plint, Amy C; Mintegi, Santiago; Klassen, Terry P; Salvadori, Marina I; Malley, Richard; Payne, Daniel C; Simon, Norma-Jean; Yock-Corrales, Adriana; Nebhrajani, Jasmine R; Chaudhari, Pradip P; Breslin, Kristen A; Finkelstein, Yaron; Campos, Carmen; Bergmann, Kelly R; Bhatt, Maala; Ahmad, Fahd A; Gardiner, Michael A; Avva, Usha R; Shah, Nipam P; Sartori, Laura F; Sabhaney, Vikram J; Caperell, Kerry; Navanandan, Nidhya; Borland, Meredith L; Morris, Claudia R; Gangoiti, Iker; Pavlicich, Viviana; Kannikeswaran, Nirupama; Lunoe, Maren M; Rino, Pedro B; Kam, April J; Cherry, Jonathan C; Rogers, Alexander J; Chong, Shu-Ling; Palumbo, Laura; Angelats, Carlos M; Morrison, Andrea K; Kwok, Maria Y; Becker, Sarah M; Dixon, Andrew C; Poonai, Naveen; Eckerle, Michelle; Wassem, Muhammad; Dalziel, Stuart R; Freedman, Stephen B

Post-COVID-19 Conditions Among Children 90 Days After SARS-CoV-2 Infection

SARS-CoV-2感染后90天儿童的COVID-19后遗症

Funk, Anna L; Kuppermann, Nathan; Florin, Todd A; Tancredi, Daniel J; Xie, Jianling; Kim, Kelly; Finkelstein, Yaron; Neuman, Mark I; Salvadori, Marina I; Yock-Corrales, Adriana; Breslin, Kristen A; Ambroggio, Lilliam; Chaudhari, Pradip P; Bergmann, Kelly R; Gardiner, Michael A; Nebhrajani, Jasmine R; Campos, Carmen; Ahmad, Fahd A; Sartori, Laura F; Navanandan, Nidhya; Kannikeswaran, Nirupama; Caperell, Kerry; Morris, Claudia R; Mintegi, Santiago; Gangoiti, Iker; Sabhaney, Vikram J; Plint, Amy C; Klassen, Terry P; Avva, Usha R; Shah, Nipam P; Dixon, Andrew C; Lunoe, Maren M; Becker, Sarah M; Rogers, Alexander J; Pavlicich, Viviana; Dalziel, Stuart R; Payne, Daniel C; Malley, Richard; Borland, Meredith L; Morrison, Andrea K; Bhatt, Maala; Rino, Pedro B; Beneyto Ferre, Isabel; Eckerle, Michelle; Kam, April J; Chong, Shu-Ling; Palumbo, Laura; Kwok, Maria Y; Cherry, Jonathan C; Poonai, Naveen; Waseem, Muhammad; Simon, Norma-Jean; Freedman, Stephen B

Pregnancy and Breastfeeding in Nephropathic Cystinosis With Native Kidneys

肾病性胱氨酸病伴原发性肾脏患者的妊娠和哺乳

Chan, Lillian; Wichart, Jenny; Kiang, Tony; Khurana, Rshmi; Gangoiti, Jon A; Barshop, Bruce A; Midgley, Julian

Tumor metabolism and neurocognition in CNS lymphoma

中枢神经系统淋巴瘤的肿瘤代谢和神经认知

Geng, Huimin; Tsang, Mazie; Subbaraj, Lakshmipriya; Cleveland, Joseph; Chen, Lingjing; Lu, Ming; Sharma, Jigyasa; Vigneron, Daniel B; Kurhanewicz, John; LaFontaine, Marisa; Luks, Tracy; Barshop, Bruce A; Gangoiti, Jon; Villanueva-Meyer, Javier E; Rubenstein, James L

Inhibition of phosphodiesterase type 9 reduces obesity and cardiometabolic syndrome in mice

抑制9型磷酸二酯酶可减轻小鼠的肥胖和心血管代谢综合征。

Sumita Mishra,Nandhini Sadagopan,Brittany Dunkerly-Eyring,Susana Rodriguez,Dylan C Sarver,Ryan P Ceddia,Sean A Murphy,Hildur Knutsdottir,Vivek P Jani,Deepthi Ashok,Christian U Oeing,Brian O'Rourke,Jon A Gangoiti,Dorothy D Sears,G William Wong,Sheila Collins,David A Kass

Lessons from the COVID-19 air pollution decrease in Spain: Now what?

从西班牙新冠疫情导致空气污染下降中汲取的经验教训:接下来该怎么做?

Querol, Xavier; Massagué, Jordi; Alastuey, Andrés; Moreno, Teresa; Gangoiti, Gotzon; Mantilla, Enrique; Duéguez, José Jaime; Escudero, Miguel; Monfort, Eliseo; Pérez García-Pando, Carlos; Petetin, Hervé; Jorba, Oriol; Vázquez, Víctor; de la Rosa, Jesús; Campos, Alberto; Muñóz, Marta; Monge, Silvia; Hervás, María; Javato, Rebeca; Cornide, María J