Randomized Clinical Trial on the Long-Term Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1
鲁马西兰治疗原发性高草酸尿症1型患者的长期疗效和安全性随机临床试验
期刊:Kidney International Reports
影响因子:5.7
doi:10.1016/j.ekir.2021.12.001
Hulton, Sally A; Groothoff, Jaap W; Frishberg, Yaacov; Koren, Michael J; Overcash, J Scott; Sellier-Leclerc, Anne-Laure; Shasha-Lavsky, Hadas; Saland, Jeffrey M; Hayes, Wesley; Magen, Daniella; Moochhala, Shabbir H; Coenen, Martin; Simkova, Eva; Garrelfs, Sander F; Sas, David J; Meliambro, Kristin A; Ngo, Taylor; Sweetser, Marianne T; Habtemariam, Bahru A; Gansner, John M; McGregor, Tracy L; Lieske, John C