日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV9 gene therapy optimization for SMARD1/CMT2S: safety and long-term efficacy comparison of two vectors in a SMARD1 preclinical model

针对SMARD1/CMT2S的AAV9基因治疗优化:在SMARD1临床前模型中比较两种载体的安全性和长期疗效

Pagliari, Elisa; Anastasia, Alessia; Bellandi, Floriana; Garbellini, Manuela; Ongaro, Jessica; Taiana, Michela; Comi, Giacomo P; Ottoboni, Linda; Sierra-Delgado, Julieth Andrea; Likhite, Shibi; Meyer, Kathrin C; Nizzardo, Monica; Corti, Stefania P

Mitochondrial Dysregulation and Impaired Autophagy in iPSC-Derived Dopaminergic Neurons of Multiple System Atrophy.

多系统萎缩症中iPSC衍生多巴胺能神经元的线粒体功能失调和自噬受损

Monzio Compagnoni Giacomo, Kleiner Giulio, Samarani Maura, Aureli Massimo, Faustini Gaia, Bellucci Arianna, Ronchi Dario, Bordoni Andreina, Garbellini Manuela, Salani Sabrina, Fortunato Francesco, Frattini Emanuele, Abati Elena, Bergamini Christian, Fato Romana, Tabano Silvia, Miozzo Monica, Serratto Giulia, Passafaro Maria, Deleidi Michela, Silipigni Rosamaria, Nizzardo Monica, Bresolin Nereo, Comi Giacomo P, Corti Stefania, Quinzii Catarina M, Di Fonzo Alessio