One-year pilot study on the effects of nitisinone on melanin in patients with OCA-1B
一项为期一年的关于尼替西酮对OCA-1B患者黑色素影响的试点研究
期刊:JCI Insight
影响因子:6.1
doi:10.1172/jci.insight.124387
Adams, David R; Menezes, Supriya; Jauregui, Ramon; Valivullah, Zaheer M; Power, Bradley; Abraham, Maria; Jeffrey, Brett G; Garced, Angel; Alur, Ramakrishna P; Cunningham, Denise; Wiggs, Edythe; Merideth, Melissa A; Chiang, Pei-Wen; Bernstein, Shanna; Ito, Shosuke; Wakamatsu, Kazumasa; Jack, Rhona M; Introne, Wendy J; Gahl, William A; Brooks, Brian P