PAXIS: A Randomized, Double-Blind, Placebo-Controlled, Dose-Finding Phase 2 Study (Part 1) Followed by an Open-Label Period (Part 2) to Assess the Efficacy and Safety of Pacritinib in Patients with VEXAS Syndrome
PAXIS：一项随机、双盲、安慰剂对照、剂量探索性 II 期研究（第一部分）及后续开放标签期（第二部分），旨在评估帕克替尼治疗 VEXAS 综合征患者的疗效和安全性
期刊:Journal of Clinical Medicine
影响因子:2.9
doi:10.3390/jcm15041426
Beck, David B; Heiblig, Maël; Savic, Sinisa; Ferrada, Marcela A; Mekinian, Arsène; Chowdhury, Onima; Hammond, Danielle; Weeks, Lachelle D; Gurnari, Carmelo; Kirino, Yohei; Georgin-Lavialle, Sophie; Buckley, Sarah A; Garcha, Raman; Harder, Bryan G; Koster, Matthew J
