Allogeneic stem cell transplantation from variant-carrying family donors leads to long-term engraftment in Telomere Biology Disorders
来自携带变异基因的家族供体的异基因干细胞移植可导致端粒生物学疾病患者的长期植入。
期刊:Blood Cancer Journal
影响因子:11.6
doi:10.1038/s41408-025-01348-z
Güzel, Nergis; Schumacher, Yannic; Kricheldorf, Kim; Vieri, Margherita; Kirschner, Martin; Gerhard-le Gars, Anne-Claire; Panse, Jens; Tometten, Mareike; Walter, Jeanette; Gehrig, Andrea; Kunstmann, Erdmute; Holthöfer, Laura; Schweiger, Susann; Wolff, Daniel; Kraft, Florian; Elbracht, Miriam; Kurth, Ingo; Brümmendorf, Tim H; Meyer, Robert; Beier, Fabian