日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Longitudinal intravital imaging of mouse placenta

小鼠胎盘纵向活体成像

Xiaoyi Zhu, Qiang Huang, Laiming Jiang, Van-Tu Nguyen, Tri Vu, Garth Devlin, Jabbar Shaima, Xiaobei Wang, Yong Chen, Lijun Ma, Kun Xiang, Ergang Wang, Qiangzhou Rong, Qifa Zhou, Yubin Kang, Aravind Asokan, Liping Feng, Shiao-Wen D Hsu, Xiling Shen, Junjie Yao

An enhancer-based gene-therapy strategy for spatiotemporal control of cargoes during tissue repair

基于增强子的基因治疗策略,用于组织修复过程中货物的时空控制

Ruorong Yan, Valentina Cigliola, Kelsey A Oonk, Zachary Petrover, Sophia DeLuca, David W Wolfson, Andrew Vekstein, Michelle A Mendiola, Garth Devlin, Muath Bishawi, Matthew P Gemberling, Tanvi Sinha, Michelle A Sargent, Allen J York, Avraham Shakked, Paige DeBenedittis, David C Wendell, Jianhong Ou,

AAV Gene Augmentation of Truncated Complement Factor H Differentially Rescues Ocular Complement Dysregulation in a Mouse Model

截短补体因子 H 的 AAV 基因增强在小鼠模型中以差异方式挽救了眼部补体失调

Daniel Grigsby, Mikael Klingeborn, Una Kelly, Lindsey A Chew, Aravind Asokan, Garth Devlin, Sharon Smith, Lisa Keyes, Adrian Timmers, Abraham Scaria, Catherine Bowes Rickman

Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy

在杜氏肌营养不良症人源化小鼠模型中,通过 AAV-CRISPR 靶向外显子整合实现全长肌营养不良蛋白修复

Adrian Pickar-Oliver, Veronica Gough, Joel D Bohning, Siyan Liu, Jacqueline N Robinson-Hamm, Heather Daniels, William H Majoros, Garth Devlin, Aravind Asokan, Charles A Gersbach

In Vivo Gene Editing of Muscle Stem Cells with Adeno-Associated Viral Vectors in a Mouse Model of Duchenne Muscular Dystrophy

在杜氏肌营养不良症小鼠模型中利用腺相关病毒载体对肌肉干细胞进行体内基因编辑

Jennifer B Kwon, Adarsh R Ettyreddy, Ashish Vankara, Joel D Bohning, Garth Devlin, Stephen D Hauschka, Aravind Asokan, Charles A Gersbach