Nonclinical Safety Profile of Revusiran, a 1st-Generation GalNAc-siRNA Conjugate for Treatment of Hereditary Transthyretin-Mediated Amyloidosis
Revusiran(一种用于治疗遗传性转甲状腺素蛋白介导的淀粉样变性的第一代 GalNAc-siRNA 偶联物)的非临床安全性概况
期刊:Nucleic Acid Therapeutics
影响因子:4.7
doi:10.1089/nat.2019.0796
Sutherland, Jessica E; Hettinger, Julia L; Chan, Amy; Gilbert, Jason; Warner, Garvin L; Davis, Wendell P