日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV-mediated gene therapy in a model of SLC13A5 citrate transporter disorder rescues epileptic and metabolic phenotypes.

在 SLC13A5 柠檬酸转运蛋白疾病模型中,AAV 介导的基因治疗可挽救癫痫和代谢表型。

Bailey Lauren E, Adams Raegan M, Schackmuth Morgan K, Garza Irvin T, Knight Krishanna, Holmes Sydni K, Eller Meghan M, Lee MinJae, Bailey Rachel M

Expression and distribution of rAAV9 intrathecally administered in juvenile to adolescent mice.

rAAV9鞘内注射入幼年至青春期小鼠体内的表达和分布

Garza Irvin T, Eller Meghan M, Holmes Sydni K, Schackmuth Morgan K, Bailey Rachel M

Preclinical Development of a Vectorized Artificial miRNA Gene Therapy for Tauopathies

针对tau蛋白病的载体化人工miRNA基因疗法的临床前开发

Garza, Irvin T; Snyder, Brina; Holmes, Sydni K; Pearce, Katherine M; Knight, Krishanna; Bailey, Rachel M