日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Long-Term Safety Evaluation of Continuous Intraocular Delivery of Aflibercept by the Intravitreal Gene Therapy Candidate ADVM-022 in Nonhuman Primates

在非人灵长类动物中,通过玻璃体内基因治疗候选药物 ADVM-022 持续眼内递送阿柏西普的长期安全性评估

Kiss, Szilárd; Oresic Bender, Kristina; Grishanin, Ruslan N; Hanna, Kelly M; Nieves, Julio D; Sharma, Pallavi; Nguyen, Aivan T; Rosario, Romeo J; Greengard, Judith S; Gelfman, Claire M; Gasmi, Mehdi

Analysis of Aflibercept Expression in NHPs following Intravitreal Administration of ADVM-022, a Potential Gene Therapy for nAMD.

对非人灵长类动物玻璃体内注射 ADVM-022(一种潜在的 nAMD 基因疗法)后 Aflibercept 表达的分析

Kiss Szilárd, Grishanin Ruslan, Nguyen Aivan, Rosario Romeo, Greengard Judith S, Nieves Julio, Gelfman Claire M, Gasmi Mehdi

Gene expression profiling of patient-derived pancreatic cancer xenografts predicts sensitivity to the BET bromodomain inhibitor JQ1: implications for individualized medicine efforts

患者来源的胰腺癌异种移植的基因表达谱可预测对 BET 溴结构域抑制剂 JQ1 的敏感性:对个性化医疗努力的意义

Benjamin Bian, Martin Bigonnet, Odile Gayet, Celine Loncle, Aurélie Maignan, Marine Gilabert, Vincent Moutardier, Stephane Garcia, Olivier Turrini, Jean-Robert Delpero, Marc Giovannini, Philippe Grandval, Mohamed Gasmi, Mehdi Ouaissi, Veronique Secq, Flora Poizat, Rémy Nicolle, Yuna Blum, Laetitia M

Long-term reversal of cholinergic neuronal decline in aged non-human primates by lentiviral NGF gene delivery

通过慢病毒载体递送NGF基因,可长期逆转老年非人灵长类动物胆碱能神经元的衰退。

Nagahara, Alan H; Bernot, Tim; Moseanko, Rod; Brignolo, Laurie; Blesch, Armin; Conner, James M; Ramirez, Anthony; Gasmi, Mehdi; Tuszynski, Mark H

Intraparenchymal spinal cord delivery of adeno-associated virus IGF-1 is protective in the SOD1G93A model of ALS

在SOD1G93A ALS模型中,脊髓实质内注射腺相关病毒IGF-1具有保护作用。

Lepore, Angelo C; Haenggeli, Christine; Gasmi, Mehdi; Bishop, Kathie M; Bartus, Raymond T; Maragakis, Nicholas J; Rothstein, Jeffrey D