Intraputaminal Gene Delivery in Two Patients with Aromatic L-Amino Acid Decarboxylase Deficiency
两例芳香族L-氨基酸脱羧酶缺乏症患者的壳核内基因递送
期刊:Movement Disorders Clinical Practice
影响因子:2.7
doi:10.1002/mdc3.13685
François-Heude, Marie-Céline; Poulen, Gaetan; Flamand Roze, Emmanuel; Nguyen Morel, Marie-Ange; Gras, Domitille; Roch-Toreilles, Isabelle; Quintard, Adeline; Baroux, Gaelle; Meyer, Pierre; Coubes, Philippe; Milesi, Christophe; Cambonie, Gilles; Baleine, Julien; Sola, Chrystelle; Delye, Bénédicte; Dimopoulou, Evgenia; Sanchez, Stéphanie; Gasnier, Mathieu; Touati, Souad; Zamora, Alberto; Pontal, Daniel; Leboucq, Nicolas; Kouyoumdjian, Virginie; Lebasnier, Adrien; Sanquer, Sylvia; Mariano-Goulart, Denis; Roujeau, Thomas; Roubertie, Agathe