日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Advances in Gene Therapy for Inherited Haemoglobinopathies

遗传性血红蛋白病基因治疗进展

Gaspar, Anna B; Gaspar, H Bobby

Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant

基于抗CD45 PBD的抗体药物偶联物是基因治疗和干细胞移植的有效靶向预处理剂。

Yeung, Jenny; Liao, Aiyin; Shaw, Matthew; Silva, Soraia; Vetharoy, Winston; Rico, Diego Leon; Kirby, Ian; Zammarchi, Francesca; Havenith, Karin; de Haan, Lolke; van Berkel, Patrick H; Sebire, Neil; Ogunbiyi, Olumide K; Booth, Claire; Gaspar, H Bobby; Thrasher, Adrian J; Chester, Kerry A; Amrolia, Persis J

Targeting the central nervous system in lysosomal storage diseases: Strategies to deliver therapeutics across the blood-brain barrier

溶酶体贮积症中枢神经系统靶向治疗:跨越血脑屏障的药物递送策略

Critchley, Bethan J; Gaspar, H Bobby; Benedetti, Sara

Genome Sequences and Characterization of Chicken Astrovirus and Avian Nephritis Virus from Tanzanian Live Bird Markets

坦桑尼亚活禽市场鸡星状病毒和禽肾炎病毒的基因组序列及特征分析

Kariithi, Henry M; Volkening, Jeremy D; Chiwanga, Gaspar H; Pantin-Jackwood, Mary J; Msoffe, Peter L M; Suarez, David L

Molecular Characterization of Complete Genome Sequence of an Avian Coronavirus Identified in a Backyard Chicken from Tanzania

对坦桑尼亚后院鸡体内发现的禽冠状病毒的完整基因组序列进行分子表征

Kariithi, Henry M; Volkening, Jeremy D; Chiwanga, Gaspar H; Goraichuk, Iryna V; Msoffe, Peter L M; Suarez, David L

Virulent Newcastle disease virus genotypes V.3, VII.2, and XIII.1.1 and their coinfections with infectious bronchitis viruses and other avian pathogens in backyard chickens in Tanzania

坦桑尼亚散养鸡中强毒新城疫病毒基因型 V.3、VII.2 和 XIII.1.1 及其与传染性支气管炎病毒和其他禽类病原体的共感染

Henry M Kariithi, Jeremy D Volkening, Gaspar H Chiwanga, Iryna V Goraichuk, Tim L Olivier, Peter L M Msoffe, David L Suarez

Author Correction: Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome

作者更正:慢病毒造血干/祖细胞基因疗法治疗威斯科特-奥尔德里奇综合征的长期安全性和有效性

Magnani, A; Semeraro, M; Adam, F; Booth, C; Dupré, L; Morris, E C; Gabrion, A; Roudaut, C; Borgel, D; Toubert, A; Clave, E; Abdo, C; Gorochov, G; Petermann, R; Guiot, M; Miyara, M; Moshous, D; Magrin, E; Denis, A; Suarez, F; Lagresle, C; Roche, A M; Everett, J; Trinquand, A; Guisset, M; Bayford, J Xu; Hacein-Bey-Abina, S; Kauskot, A; Elfeky, R; Rivat, C; Abbas, S; Gaspar, H B; Macintyre, E; Picard, C; Bushman, F D; Galy, A; Fischer, A; Six, E; Thrasher, A J; Cavazzana, M

Long-Term Immune Recovery After Hematopoietic Stem Cell Transplantation for ADA Deficiency: a Single-Center Experience

ADA缺陷患者接受造血干细胞移植后的长期免疫重建:单中心经验

Kreins, Alexandra Y; Velasco, Helena F; Cheong, Kai-Ning; Rao, Kanchan; Veys, Paul; Worth, Austen; Gaspar, H Bobby; Booth, Claire

Retrospective, Landmark Analysis of Long-term Adult Morbidity Following Allogeneic HSCT for Inborn Errors of Immunity in Infancy and Childhood

回顾性里程碑分析:异基因造血干细胞移植治疗婴幼儿期先天性免疫缺陷后成人长期发病率

Day, James W; Elfeky, Reem; Nicholson, Bethany; Goodman, Rupert; Pearce, Rachel; Fox, Thomas A; Worth, Austen; Booth, Claire; Veys, Paul; Carpenter, Ben; Hough, Rachael; Gaspar, H Bobby; Titman, Penny; Ridout, Deborah; Workman, Sarita; Hernandes, Fernando; Sandford, Kit; Laurence, Arian; Campbell, Mari; Burns, Siobhan O; Morris, Emma C

Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency

自体体外慢病毒基因疗法治疗腺苷脱氨酶缺乏症

Kohn, Donald B; Booth, Claire; Shaw, Kit L; Xu-Bayford, Jinhua; Garabedian, Elizabeth; Trevisan, Valentina; Carbonaro-Sarracino, Denise A; Soni, Kajal; Terrazas, Dayna; Snell, Katie; Ikeda, Alan; Leon-Rico, Diego; Moore, Theodore B; Buckland, Karen F; Shah, Ami J; Gilmour, Kimberly C; De Oliveira, Satiro; Rivat, Christine; Crooks, Gay M; Izotova, Natalia; Tse, John; Adams, Stuart; Shupien, Sally; Ricketts, Hilory; Davila, Alejandra; Uzowuru, Chilenwa; Icreverzi, Amalia; Barman, Provaboti; Campo Fernandez, Beatriz; Hollis, Roger P; Coronel, Maritess; Yu, Allen; Chun, Krista M; Casas, Christian E; Zhang, Ruixue; Arduini, Serena; Lynn, Frances; Kudari, Mahesh; Spezzi, Andrea; Zahn, Marco; Heimke, Rene; Labik, Ivan; Parrott, Roberta; Buckley, Rebecca H; Reeves, Lilith; Cornetta, Kenneth; Sokolic, Robert; Hershfield, Michael; Schmidt, Manfred; Candotti, Fabio; Malech, Harry L; Thrasher, Adrian J; Gaspar, H Bobby