日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Non-neurological, non-skeletal outcomes after hematopoietic stem and progenitor cell-gene therapy (OTL-203) for Hurler syndrome

造血干细胞和祖细胞基因治疗(OTL-203)治疗赫勒综合征的非神经系统、非骨骼结局

Tucci, Francesca; Uria Oficialdegui, M Luz; Consiglieri, Giulia; Cossutta, Matilde; Filisetti, Chiara; Fumagalli, Francesca; Butera, Carla; Santangelo, Roberto; Colombo, Michele; Manitto, Maria Pia; Stoppani, Monica; Martina, Elisabetta; Danè, Giulia; Camesasca, Chiara; Risca, Giulia; De Pellegrin, Maurizio; Scarparo, Stefano; Sarzana, Marina; Puricelli, Cristina; Galimberti, Stefania; Darin, Silvia; Silvani, Paolo; Bonanomi, Sonia; Gasperini, Serena; Naldini, Luigi; Gentner, Bernhard; Parini, Rossella; Del Toro, Mireia; Diaz-de-Heredia, Cristina; Aiuti, Alessandro; Bernardo, Maria Ester

Treg Susceptibility to Cladribine-Induced Depletion Correlates With Therapy Response in Patients With Multiple Sclerosis

Treg细胞对克拉屈滨诱导耗竭的敏感性与多发性硬化症患者的治疗反应相关

Cammarata, Ilenia; Sartori, Giorgia; Giacomelli, Tiziano; Pinna, Valeria; Pinzon Grimaldos, Alessandra; De Rosa, Giusy; Matarese, Giuseppe; Procaccini, Claudio; Mishra, Divya; Di Mitri, Diletta; Gasperini, Claudio; Guerrera, Gisella; Sambucci, Manolo; Battistini, Luca; Piconese, Silvia

The new earthquake locations and focal mechanisms catalogues for the western Ionian Sea, Italy

意大利爱奥尼亚海西部地区新的地震位置和震源机制目录

Sgroi, Tiziana; Barberi, Graziella; Marchetti, Alessandro; Gasperini, Luca; Polonia, Alina

Can Alpha-Glucosidase Activity in Plasma or Leukocytes Serve as a Biomarker for Future Gene Therapy in Classic Infantile Pompe Disease?

血浆或白细胞中的α-葡萄糖苷酶活性能否作为经典婴儿型庞贝病未来基因治疗的生物标志物?

Faraguna, Martha C; Lambregts, Daniël A M; Barzel, Ina; Jacobs, Ed H; Hoogeveen-Westerveld, Marianne; van der Beek, Nadine A M E; Pijnappel, W W M Pim; Gasperini, Serena; Preijers, Tim; van den Hout, Johanna M P; van der Ploeg, Ans T

Correction: Can Alpha-Glucosidase Activity in Plasma or Leukocytes Serve as a Biomarker for Future Gene Therapy in Classic Infantile Pompe Disease?

更正:血浆或白细胞中的α-葡萄糖苷酶活性能否作为经典婴儿型庞贝病未来基因治疗的生物标志物?

Faraguna, Martha C; Lambregts, Daniël A M; Barzel, Ina; Jacobs, Ed H; Hoogeveen-Westerveld, Marianne; van der Beek, Nadine A M E; Pijnappel, W W M Pim; Gasperini, Serena; Preijers, Tim; van den Hout, Johanna M P; van der Ploeg, Ans T

A 3D model to evaluate cell chemotaxis within a heterogenic tumor microenvironment

用于评估异质性肿瘤微环境中细胞趋化性的三维模型

Rodrigues, Daniel B; Cruz-Moreira, Daniela; Gasperini, Luca; Jarnalo, Mariana; Horta, Ricardo; Reis, Rui L; Pirraco, Rogério P

Double-hit approach for novel glycoconjugates combining cytoplasmic glycoengineering and selective chemistry

结合细胞质糖工程和选择性化学的双重打击策略,用于合成新型糖缀合物

Palmieri, Elena; Monaci, Valentina; Durante, Salvatore; Cescutti, Paola; Micoli, Francesca; Gasperini, Gianmarco

Genetic diversity of alpha and betacoronaviruses in cave and temple-roosting bats in Vientiane Province, Lao PDR

老挝万象省洞穴和寺庙栖息蝙蝠体内甲型和乙型冠状病毒的遗传多样性

Mombo, Illich Manfred; Bobouaka Bonguili, Novy Charel; Gasperini, Nicola; Chandarak, Arisa; Xaiyaphoumi, Thida; Brault, Pauline; Rieu, Oceane; Paboriboune, Phimpha; Leroy, Eric; Niama, Fabien Roch; Locatelli, Sabrina

Cardiopulmonary and skeletal muscle strategies underlying exhaustive exercise in adults with glycogen storage disease type III

III型糖原贮积症成人进行剧烈运动的心肺和骨骼肌策略

Lanfranconi, F; Peli, L; Pollastri, L; Ferri, A; Tremolizzo, L; Conti, E; Pieruzzi, F; Miserocchi, G; Beretta, E; Marzorati, M; Zardo, W; Gasperini, S; Pretese, R; Paci, S; Capelli, C; Mariani, R; Cattoni, A; Balduzzi, A C; Parini, R

Acute Effects of Beetroot Supplementation on Resistance Exercise Performance in Physically Active Men

甜菜根补充剂对活跃男性抗阻运动表现的急性影响

Rodrigues, Maitê Yorioka; Takito, Monica Yuri; Kafouri, Gabriel Albanese; Pires, Rebeca Soares; Mello, Felipe Gasperini; Zare, Reza; Hernandez, Sthefano Ventura; Heinrich, Katie M; Franchini, Emerson