Similarities and Differences in the Late-Onset GM2 Gangliosidoses: Tay-Sachs and Sandhoff Diseases
晚发型GM2神经节苷脂沉积症的异同:泰-萨克斯病和桑德霍夫病
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doi:10.1101/2025.08.05.25333048
Lewis, Connor J; Shirvan, Leila; Johnston, Jean M; Groden, Catherine; Yang, John; Ashton, Andrea; Chong, Jessica; Moran, Mark; Akmal, Hera; Chipman, Selby I; Zampieri, Cris; Wickstrom, Jordan; Matsubara, Jesse; Gavelli, Frances; Lehky, Tanya; Alter, Katharine E; Toro, Camilo; Tifft, Cynthia J