日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

作者更正:鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Integration of plasma eMTBR-tau243 and p-tau217 in the diagnosis and stratification of Alzheimer's disease: a prospective cohort study

整合血浆eMTBR-tau243和p-tau217进行阿尔茨海默病诊断和分层:一项前瞻性队列研究

Mattsson-Carlgren, Niklas; Palmqvist, Sebastian; Horie, Kanta; Barthélemy, Nicolas; Salvadó, Gemma; Binette, Alexa Pichet; Tideman, Pontus; Morris, John C; Benzinger, Tammie Ls; Perrin, Richard J; Janelidze, Shorena; Collij, Lyduine E; Ossenkoppele, Rik; Schindler, Suzanne E; Stomrud, Erik; Bateman, Randall J; Hansson, Oskar

Assessment and Optimization of 2T Perovskite/CIGS Tandems via Data-Driven and Optoelectronic Modelling

基于数据驱动和光电建模的2T钙钛矿/CIGS串联器件的评估与优化

Giliberti, Gemma; Farias-Basulto, Guillermo; Jäger, Klaus; Mehlhop, Thede; Kaufmann, Christian A; Di Carlo, Aldo

The stroke risk gene Foxf2 maintains brain endothelial cell function via Tie2 signaling

中风风险基因Foxf2通过Tie2信号通路维持脑内皮细胞功能。

Todorov-Völgyi, Katalin; González-Gallego, Judit; Müller, Stephan A; Todorov, Mihail Ivilinov; Seker, Fatma Burcu; Frerich, Simon; Cernilogar, Filippo M; Schröger, Luise; Malik, Rainer; Cao, Jiayu; Llovera, Gemma; Roth, Stefan; Schillinger, Ulrike; Schifferer, Martina; Reyahi, Azadeh; Crusius, Dennis; Pedro, Liliana D; Simons, Mikael; Carlsson, Peter; Ertürk, Ali; Liesz, Arthur; Schotta, Gunnar; Plesnila, Nikolaus; Lichtenthaler, Stefan F; Paquet, Dominik; Dichgans, Martin

Pragmatic representations of self- and others' action in the monkey putamen

猴子壳核中对自我和他人行为的实用性表征

Rotunno, Cristina; Reni, Matilde; Ferroni, Carolina Giulia; Ismaiel, Ebrahim; Ballestrazzi, Gemma; Borra, Elena; Maranesi, Monica; Bonini, Luca

Trajectories of plasma and CSF MTBR-tau243 and phosphorylated-tau species across the Alzheimer's disease continuum

阿尔茨海默病连续谱中血浆和脑脊液中MTBR-tau243和磷酸化tau蛋白的变化轨迹

Collij, Lyduine E; Salvadó, Gemma; Horie, Kanta; Barthélemy, Nicolas R; Betthauser, Tobey J; Strandberg, Olof; Smith, Ruben; Palmqvist, Sebastian; Schindler, Suzanne E; Ossenkoppele, Rik; Janelidze, Shorena; Mattsson-Carlgren, Niklas; Bateman, Randall J; Hansson, Oskar

Coronaviruses reprogram the tRNA epitranscriptome to favor viral protein expression.

冠状病毒会重编程 tRNA 表观转录组,以促进病毒蛋白的表达。

Muscolino Elena, Puig-Torrents Mireia, Buigues Bisquert Jaime, Correa Mendonca Diogo, Talló-Parra Marc, Perez-Vilaro Gemma, Caño-Prades Omar, Meehan Gavin R, Kerr Karen, Herder Vanessa, Chillón Miguel, Castello Alfredo, Sanjuan Rafael, Patel Arvind H, Díez Juana

Reduction of RAD23A extends lifespan and mitigates pathology in a mouse model of TDP-43 proteinopathy.

RAD23A 的减少可延长 TDP-43 蛋白病小鼠模型的寿命并减轻病理。

Guo Xueshui, Prajapati Ravindra Singh, Chun Jiyeon, Byun Insuk, Gebis Kamil K, Wang Yi-Zhi, Ling Karen, Dalton Casey, Blair Jeff A, Hamidianjahromi Anahid, Bachmann Gemma, Rigo Frank, Jafar-Nejad Paymaan, Savas Jeffrey N, Lee Min Jae, Sreedharan Jemeen, Kalb Robert G

Oxidation of a Dihydrophenazine Molecular Wire Attenuates Molecular Conductance

二氢吩嗪分子导线的氧化会降低分子电导率

Nau, Moritz; Ahmed, Raka; Leitherer, Susanne; Solomon, Gemma C; Winter, Rainer F