日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Long-Term Tofersen in SOD1 Amyotrophic Lateral Sclerosis

托弗森治疗SOD1肌萎缩侧索硬化症的长期疗效

Miller, Timothy M; Cudkowicz, Merit E; Shaw, Pamela J; Genge, Angela; Sobue, Gen; Bucelli, Robert C; Chiò, Adriano; Van Damme, Philip; Ludolph, Albert C; Glass, Jonathan D; Andrews, Jinsy A; Babu, Suma; Benatar, Michael; McDermott, Christopher J; Salachas, François; Bruneteau, Gaëlle; Al-Chalabi, Ammar; Amorin, Matthew; Nestorov, Ivan; Graham, Danielle; Lin, Luan; Sun, Peng; McNeill, Manjit; Malek, Sohail; Inra, Jennifer; Garafalo, Steve; Fradette, Stephanie

Heterogeneity in the Analysis of the ALSFRS-R in ALS Clinical Trials and its Effect on the Validity and Precision of Trial Conclusions

ALS临床试验中ALSFRS-R分析的异质性及其对试验结论的有效性和精确性的影响

Weemering, Daphne N; van Unnik, Jordi W J; Genge, Angela; van den Berg, Leonard H; van Eijk, Ruben P A

Progressive and Short-Interval Changes Observed in the Corticospinal Tract and Corpus Callosum of Patients with Amyotrophic Lateral Sclerosis: A Texture Analysis Study

肌萎缩侧索硬化症患者皮质脊髓束和胼胝体进行性及短期变化的纹理分析研究

Parnianpour, Pedram; Harrison, Matthew; Benatar, Michael; Briemberg, Hannah; Dionne, Annie; Dupré, Nicolas; Frayne, Richard; Genge, Angela; Graham, Simon J; Korngut, Lawrence; Seres, Peter; Wilman, Alan; Zinman, Lorne; Kalra, Sanjay

Safety of Intravenous Edaravone in Clinical Practice

临床实践中静脉注射依达拉奉的安全性

Genge, Angela; Apple, Stephen

Phase 3b Extension Study MT-1186-A04 to Evaluate the Continued Efficacy and Safety of Edaravone Oral Suspension for Up to an Additional 48 Weeks in Patients With Amyotrophic Lateral Sclerosis

MT-1186-A04 3b 期扩展研究旨在评估依达拉奉口服混悬液在肌萎缩侧索硬化症患者中持续 48 周的疗效和安全性

Genge, Angela; Rothstein, Jeffrey; De Silva, Shari; Zinman, Lorne; Chum, Marvin; Chiò, Adriano; Sobue, Gen; Aoki, Masashi; Yoshino, Hiide; Doyu, Manabu; Selness, Daniel; Todorovic, Vesna; Hirai, Manabu; Sasson, Nissim; Takahashi, Fumihiro; Cecić, Michelle; Wamil, Art; Apple, Stephen

Reldesemtiv in Amyotrophic Lateral Sclerosis: Results From the COURAGE-ALS Randomized Clinical Trial

Reldesemtiv治疗肌萎缩侧索硬化症:COURAGE-ALS随机临床试验结果

Shefner, Jeremy M; Cudkowicz, Merit E; Genge, Angela; Hardiman, Orla; Al-Chalabi, Ammar; Andrews, Jinsy A; Chio, Adriano; Corcia, Philippe; Couratier, Philippe; de Carvalho, Mamede; Heiman-Patterson, Terry; Henderson, Robert D; Ingre, Caroline; Johnston, Wendy; Ludolph, Albert; Maragakis, Nicholas J; Miller, Timothy M; Mora, Jesus S; Petri, Susanne; Simmons, Zachary; van den Berg, Leonard H; Zinman, Lorne; Kupfer, Stuart; Malik, Fady I; Meng, Lisa; Simkins, Tyrell J; Wei, Jenny; Wolff, Andrew A; Rudnicki, Stacy A

Changes in corticosteroid and non-steroidal immunosuppressive therapy with long-term zilucoplan treatment in generalized myasthenia gravis

长期使用齐鲁普兰治疗全身型重症肌无力时,皮质类固醇和非甾体类免疫抑制剂治疗方案的变化

Hewamadduma, Channa; Freimer, Miriam; Genge, Angela; Leite, M Isabel; Utsugisawa, Kimiaki; Vu, Tuan; Boroojerdi, Babak; Grimson, Fiona; Savic, Natasa; Vanderkelen, Mark; Howard, James F Jr

Efficacy and Safety of Once Daily Dosing vs. Approved On/Off Dosing of Edaravone Oral Suspension Up to 48 Weeks in Patients With Amyotrophic Lateral Sclerosis (Study MT-1186-A02)

肌萎缩侧索硬化症患者每日一次给药与批准的间歇性给药方案(依达拉奉口服混悬液)长达 48 周的疗效和安全性比较(MT-1186-A02 研究)

Rothstein, Jeffrey; Genge, Angela; De Silva, Shari; Zinman, Lorne; Chum, Marvin; Chio, Adriano; Sobue, Gen; Aoki, Masashi; Yoshino, Hiide; Doyu, Manabu; Selness, Daniel; Todorovic, Vesna; Sasson, Nissim; Hirai, Manabu; Takahashi, Fumihiro; Salah, Alejandro; Wamil, Art; Apple, Stephen

Safety Extension Study of Edaravone Oral Suspension in Patients With Amyotrophic Lateral Sclerosis for up to an Additional 96 Weeks of Treatment

一项针对肌萎缩侧索硬化症患者的依达拉奉口服混悬液安全性扩展研究,疗程最长可达96周

Genge, Angela; Pattee, Gary L; Sobue, Gen; Aoki, Masashi; Yoshino, Hiide; Couratier, Philippe; Lunetta, Christian; Petri, Susanne; Selness, Daniel; Todorovic, Vesna; Sasson, Nissim; Hirai, Manabu; Takahashi, Fumihiro; Salah, Alejandro; Apple, Stephen; Wamil, Art; Kalin, Alexander; Jackson, Carlayne E

Analysis of Long-Term Function and Survival of Edaravone Oral Suspension-Treated Patients With Amyotrophic Lateral Sclerosis Using PRO-ACT Data as Historical Placebo Controls

利用 PRO-ACT 数据作为历史安慰剂对照,分析依达拉奉口服混悬液治疗肌萎缩侧索硬化症患者的长期功能和生存情况

Takahashi, Fumihiro; Genge, Angela; Hirai, Manabu; Selness, Daniel; Todorovic, Vesna; Wamil, Art; Sasson, Nissim; Apple, Stephen; Ushirogawa, Yoshiteru