Phenotypic Correction of Murine Mucopolysaccharidosis Type II by Engraftment of Ex Vivo Lentiviral Vector-Transduced Hematopoietic Stem and Progenitor Cells
通过体外慢病毒载体转导的造血干细胞和祖细胞植入对小鼠粘多糖贮积症 II 型进行表型校正
期刊:Human Gene Therapy
影响因子:3.9
doi:10.1089/hum.2022.141
Miles C Smith, Lalitha R Belur, Andrea D Karlen, Olivia Erlanson, Kelly M Podetz-Pedersen, Jessica McKenzie, Jenn Detellis, Khatuna Gagnidze, Geoffrey Parsons, Nicholas Robinson, Shelby Labarre, Saumil Shah, Justin Furcich, Troy C Lund, Hsing-Chen Tsai, R Scott McIvor, Melissa Bonner
