Augmentation Therapy for Severe Alpha-1 Antitrypsin Deficiency Improves Survival and Is Decoupled from Spirometric Decline-A Multinational Registry Analysis
一项多国注册研究分析表明,针对重度α1-抗胰蛋白酶缺乏症的增强疗法可提高生存率,且与肺功能下降无关。
期刊:American Journal of Respiratory and Critical Care Medicine
影响因子:19.4
doi:10.1164/rccm.202305-0863OC
Fraughen, Daniel D; Ghosh, Auyon J; Hobbs, Brian D; Funk, Georg-Christian; Meischl, Tobias; Clarenbach, Christian F; Sievi, Noriane A; Schmid-Scherzer, Karin; McElvaney, Oliver J; Murphy, Mark P; Roche, Adam D; Clarke, Louise; Strand, Matthew; Vafai-Tabrizi, Florian; Kelly, Geraldine; Gunaratnam, Cedric; Carroll, Tomás P; McElvaney, Noel G