Amelioration of Inflammation and Metabolic Blockage in GALC Deficient Mice After Enzyme Replacement Therapy via Extracellular Vesicles.
通过细胞外囊泡进行酶替代疗法可改善 GALC 缺陷小鼠的炎症和代谢阻滞
期刊:International Journal of Nanomedicine
影响因子:6.5
doi:10.2147/IJN.S523938
Zelada Diego, Saldivia Natalia, Samano Shayla, George Diann, Chaudhari Kenvi, Nguyen Duc, Simchuk Daniel, Van Breemen Richard B, Givogri Maria Irene