日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Comparative Efficacy and Safety of Anakinra and Canakinumab in Patients With VEXAS Syndrome: An International Multicenter Study

阿那白滞素和卡那单抗治疗VEXAS综合征患者的疗效和安全性比较:一项国际多中心研究

Eviatar, Tali; Capelusnik, Dafne; Campochiaro, Corrado; Lacombe, Valentin; Jachiet, Vincent; Zisapel, Michael; Sagy, Iftach; Tayer-Shifman, Oshrat E; Ozeri, David; Kivity, Shaye; Tomelleri, Alessandro; Terrier, Benjamin; Peleg, Hagit; Comont, Thibault; Sacre, Karim; Woaye-Hune, Pascal; Arnaud, Laurent; Lazaro, Estibaliz; Grobost, Vincent; Lifermann, Francois; Samson, Maxime; Ardois, Samuel; Garnier, Alice; Maria, Alexandre; Cantagrel, Alain; Meyer, Aurore; Bouaziz, Jean-David; Heiblig, Mael; Dagna, Lorenzo; Diral, Elisa; Kosmider, Olivier; Elkayam, Ori; Hadjadj, Jérôme; Georgin-Lavialle, Sophie; Fain, Olivier; Mekinian, Arsene

American College of Rheumatology Guidance Statement for Diagnosis and Management of VEXAS Developed by the International VEXAS Working Group Expert Panel

美国风湿病学会关于VEXAS诊断和治疗的指导声明,由国际VEXAS工作组专家组制定

Mekinian, Arsene; Georgin-Lavialle, Sophie; Ferrada, Marcela A; Savic, Sinisa; Koster, Matthew J; Kosmider, Olivier; Comont, Thibault; Heiblig, Mael; Arostegui, Juan I; Bosco, Annmarie; Bourguiba, Rim; Calvo, Katherine R; Cargo, Catherine; Cattaneo, Chiara; Chasset, François; Coelho, Henrique; Campochiaro, Corrado; Crisafulli, Francesca; Ducharme-Benard, Stephanie; Faria, Raquel; Franceschini, Franco; Frassi, Micol; Groarke, Emma M; Gurnari, Carmelo; Hakobyan, Yervand; Jamilloux, Yvan; Jurcut, Ciprian; Kirino, Yohei; Kulasekararaj, Austin; Kunimoto, Hiroyoshi; Madigan, Lauren M; Mann, Heřman F; Marvisi, Chiara; Milchert, Marcin; Morais, Sara; Sockel, Katja; Muratore, Francesco; Nakajima, Hideaki; Patnaik, Mrinal M; Regadas, Luísa; Robin, Marie; Rutgers, Abraham; Salvarani, Carlo; Sammel, Anthony M; Seebach, Joerg; Sujobert, Pierre; Tomelleri, Alessandro; Urbanski, Geoffrey; Vandergheynst, Frédéric; Vieira, Romana; Viswanatha, David S; Więsik-Szewczyk, Ewa; Diral, Elisa; Terrier, Benjamin; Patel, Bhavisha A; Fenaux, Pierre; Grayson, Peter C; Beck, David B

Colchicine resistance prediction criteria from the TURPAID cohort do not apply to the JIR cohort: a multicentre descriptive analysis

来自 TURPAID 队列的秋水仙碱耐药性预测标准不适用于 JIR 队列:一项多中心描述性分析

Mertz, Philippe; Elhani, Inès; Koné-Paut, Isabelle; Dan, Diana; Roque, Sandrine; Theodoropoulou, Katerina; Pachlopnick Schmid, Jana; Bader-Menier, Brigitte; Belot, Alexandre; Dumaine, Cécile; Kevorkian-Verguet, Charlotte; Cavelot, Sébastien; Georgin-Lavialle, Sophie; Hentgen, Véronique

Functional changes in the gut microbiota are associated with the intestinal phenotype in A20 haploinsufficiency

肠道菌群的功能变化与A20单倍体不足的肠道表型相关

Elhani, Inès; Bredon, Marius; Enea, Diana; Desmons, Aurore; Arrive, Lionel; Bazille, Céline; Lefevre, Antoine; Aouba, Achille; Bigot, Adrien; de Moreuil, Claire; Alonso, Iria; Blasco, Hélène; Creusot, Laura; Dupuy, Camille; Emond, Patrick; Krasniqi, Pranvera; Lamaziere, Antonin; Oeuvray, Cyriane; Rainteau, Dominique; Svrcek, Magali; Rolhion, Nathalie; Sokol, Harry; Georgin-Lavialle, Sophie

PAXIS: A Randomized, Double-Blind, Placebo-Controlled, Dose-Finding Phase 2 Study (Part 1) Followed by an Open-Label Period (Part 2) to Assess the Efficacy and Safety of Pacritinib in Patients with VEXAS Syndrome

PAXIS:一项随机、双盲、安慰剂对照、剂量探索性 II 期研究(第一部分)及后续开放标签期(第二部分),旨在评估帕克替尼治疗 VEXAS 综合征患者的疗效和安全性

Beck, David B; Heiblig, Maël; Savic, Sinisa; Ferrada, Marcela A; Mekinian, Arsène; Chowdhury, Onima; Hammond, Danielle; Weeks, Lachelle D; Gurnari, Carmelo; Kirino, Yohei; Georgin-Lavialle, Sophie; Buckley, Sarah A; Garcha, Raman; Harder, Bryan G; Koster, Matthew J

Juvenile Inflammatory Rheumatism Real-Life Clinical Practice Strategies (JIR-CliPS) network: methodology and the development process

青少年炎症性风湿病真实世界临床实践策略(JIR-CliPS)网络:方法论和发展过程

Wittkowski, Helmut; Carlomagno, Raffaella; Georgin-Lavialle, Sophie; Costa Duarte Lanna, Cristina; Dey, Dzifa; Frank, Marie; Gorczyca, Daiva; Hofer, François; Kallinich, Tilmann; Kamphuis, Sylvia; Riley, Phil; Rodrigues, Mariana; Sahin, Sezgin; Snipaitiene, Ausra; Theodoropoulou, Katerina; Toplak, Natasa; Yan, Jacqueline; Hofer, Michaël; Hentgen, Véronique

Inflammatory disorders in IDH-mutated myeloid neoplasms: Characteristics and response to IDH inhibitors

IDH突变型髓系肿瘤的炎症性疾病:特征及对IDH抑制剂的反应

Stammler, Romain; Chen, Peter; Debeaupuis, Orianne; Zhao, Lin-Pierre; Ruyer-Thompson, Mirabelle; Zakine, Eve; Rossignol, Julien; Goldwirt, Lauriane; Comont, Thibault; Heiblig, Maël; Adès, Lionel; Sebert, Marie; Allain, Jean-Sébastien; Campagne, Julien; Couturier, Marie-Anne; Cumin, Marina; Dalmas, Marie-Caroline; Denis, Guillaume; Devloo, Cécile; De Voeght, Adrien; Drevon, Louis; Duffau, Pierre; Georgin-Lavialle, Sophie; Gobert, Delphine; Kosmider, Olivier; Rieux-Laucat, Frédéric; Abisror, Noémie; Lazaro, Estibaliz; Lopez, Jean-Guillaume; Maria, Alexandre; Mauhin, Wladimir; Merindol, Julie; Merlot, Claire; Mirault, Tristan; Pascal, Laurent; Perrin, François; Raffoux, Emmanuel; Rahme, Ramy; Roos-Weil, Damien; Terrier, Benjamin; Thoreau, Benjamin; Fain, Olivier; Fenaux, Pierre; Hirsch, Pierre; Jachiet, Vincent; Hadjadj, Jérôme; Mékinian, Arsène

Efficacy of erythroid-stimulating agent and luspatercept in VEXAS syndrome: A multicenter retrospective study by the FRENVEX group

红细胞刺激剂和鲁斯帕西普治疗VEXAS综合征的疗效:FRENVEX研究组的一项多中心回顾性研究

Heiblig, Maël; Jachiet, Vincent; Hadjadj, Jérôme; Zhao, Lin Pierre; Comont, Thibault; Lobbes, Hervé; Lacombe, Valentin; Boutin, Anne Blandine; Galland, Joris; Terrier, Benjamin; Georgin-Lavialle, Sophie; Fenaux, Pierre; Mekinian, Arsène

Telomere occupancy by TRF2 is altered by KIT mutations and correlates with mastocytosis regression

KIT基因突变会改变TRF2对端粒的占据情况,并且这种改变与肥大细胞增生症的消退相关。

Bruneau, Julie; Georgin-Lavialle, Sophie; Ladraa, Sophia; Belaid, Zakia; Plo, Isabelle; Letard, Sébastien; Soucie, Erinn; Draskovic, Irena; Goudin, Nicolas; Bouillié, Marie; Lepelletier, Yves; Rossignol, Julien; Polivka, Laura; Frenzel, Laurent; Lortholary, Olivier; Fraitag, Sylvie; Bodemer, Christine; Revy, Patrick; Arock, Michel; Molina, Thierry-Jo; Londono-Vallejo, Arturo; Dubreuil, Patrice; Maouche-Chretien, Leila; Hermine, Olivier

Inflammatory Signatures in VEXAS Syndrome, Myelodysplasia Cutis, and Sweet Syndrome

VEXAS综合征、皮肤骨髓增生异常综合征和Sweet综合征的炎症特征

Grolleau, Chloé; Battistella, Maxime; Zakine, Eve; Poisot, Thomas; Cordoliani, Florence; Mahevas, Thibault; Jachiet, Marie; de Masson, Adèle; Mekinian, Arsène; Terrier, Benjamin; Lavialle, Sophie Georgin; Fenaux, Pierre; Adès, Lionel; Zhao, Lin-Pierre; Serror, Kevin; Duchmann, Matthieu; Clappier, Emmanuelle; Onifarasoaniaina, Rachel; Le Buanec, Hélène; Moguelet, Philippe; Bouaziz, Jean-David; Chasset, Francois