Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation
在Omenn综合征重组激活基因2小鼠模型中,慢病毒介导的基因治疗的疗效不受炎症和免疫失调的影响。
期刊:Journal of Allergy and Clinical Immunology
影响因子:11.4
doi:10.1016/j.jaci.2017.11.015
Valentina Capo ,Maria Carmina Castiello ,Elena Fontana ,Sara Penna ,Marita Bosticardo ,Elena Draghici ,Luigi P Poliani ,Lucia Sergi Sergi ,Rosita Rigoni ,Barbara Cassani ,Monica Zanussi ,Paola Carrera ,Paolo Uva ,Kerry Dobbs ,Nicolò Sacchetti ,Luigi D Notarangelo ,Niek P van Til ,Gerard Wagemaker ,Anna Villa