日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Nanoparticle-delivered resiquimod induces brain tumor regression in medulloblastoma and diffuse midline glioma models by interrupting paracrine growth support and activating myeloid immune signaling and phagocytosis

纳米颗粒递送的瑞喹莫德可通过阻断旁分泌生长支持并激活髓系免疫信号传导和吞噬作用,诱导髓母细胞瘤和弥漫性中线胶质瘤模型中的脑肿瘤消退。

McSwain, Leon; Kim, Kyongtea; Hwang, Duhyeong; Lim, Chaemin; Winham, Cynthia; Jacques, Jon; Rosen, Elias; Kasturi, Sudhir; Pradhan, Arpan; Tikunov, Andrey; Kabanov, Alexander V; Raper, Jessica; Gershon, Timothy R; Sokolsky, Marina

ReNeu: A Pivotal, Phase IIb Trial of Mirdametinib in Adults and Children With Symptomatic Neurofibromatosis Type 1-Associated Plexiform Neurofibroma

ReNeu:一项针对有症状的1型神经纤维瘤病相关丛状神经纤维瘤成人和儿童的米达替尼关键性IIb期试验

Moertel, Christopher L; Hirbe, Angela C; Shuhaiber, Hans H; Bielamowicz, Kevin; Sidhu, Alpa; Viskochil, David; Weber, Michael D; Lokku, Armend; Smith, L Mary; Foreman, Nicholas K; Hajjar, Fouad M; McNall-Knapp, Rene Y; Weintraub, Lauren; Antony, Reuben; Franson, Andrea T; Meade, Julia; Schiff, David; Walbert, Tobias; Ambady, Prakash; Bota, Daniela A; Campen, Cynthia J; Kaur, Gurcharanjeet; Klesse, Laura J; Maraka, Stefania; Moots, Paul L; Nevel, Kathryn; Bornhorst, Miriam; Aguilar-Bonilla, Ana; Chagnon, Sarah; Dalvi, Nagma; Gupta, Punita; Khatib, Ziad; Metrock, Laura K; Nghiemphu, P Leia; Roberts, Ryan D; Robison, Nathan J; Sadighi, Zsila; Stapleton, Stacie; Babovic-Vuksanovic, Dusica; Gershon, Timothy R

Reply to: Challenges in Assessing Response in Clinical Trials for Neurofibromatosis Type 1 Plexiform Neurofibromas

回复:评估 1 型神经纤维瘤病丛状神经纤维瘤临床试验疗效的挑战

Moertel, Christopher L; Hirbe, Angela C; Klesse, Laura J; Nghiemphu, P Leia; Babovic-Vuksanovic, Dusica; Gershon, Timothy R

Suppressing recurrence in Sonic Hedgehog subgroup medulloblastoma using the OLIG2 inhibitor CT-179

使用 OLIG2 抑制剂 CT-179 抑制 Sonic Hedgehog 亚组髓母细胞瘤的复发

Li, Yuchen; Lim, Chaemin; Dismuke, Taylor; Malawsky, Daniel S; Oasa, Sho; Bruce, Zara C; Offenhäuser, Carolin; Baumgartner, Ulrich; D'Souza, Rochelle C J; Edwards, Stacey L; French, Juliet D; Ock, Lucy S H; Nair, Sneha; Sivakumaran, Haran; Harris, Lachlan; Tikunov, Andrey P; Hwang, Duhyeong; Alicea Pauneto, Coral Del Mar; Maybury, Mellissa; Hassall, Timothy; Wainwright, Brandon; Kesari, Santosh; Stein, Gregory; Piper, Michael; Johns, Terrance G; Sokolsky-Papkov, Marina; Terenius, Lars; Vukojević, Vladana; McSwain, Leon F; Gershon, Timothy R; Day, Bryan W

Sonic hedgehog medulloblastomas are dependent on Netrin-1 for survival.

音猬因子髓母细胞瘤的存活依赖于 Netrin-1

Talbot Julie, Fombonne Joanna, Torrejon Jacob, Babcock Benjamin R, McSwain Leon F, Rama Nicolas, Lospinoso Severini Ludovica, Bonerandi Emma, Marsaud Veronique, Bernardi Flavia, Gharsalli Tarek, Guix Catherine, Ducarouge Benjamin, Neururer Verena, Basili Irene, Mercier Audrey L, Yu Hua, Forget Antoine, Indersie Emilie, Leboucher Sophie, Souphron Judith, Okonechnikov Konstantin, Wang Wanchen, Kawauchi Daisuke, Wainwright Brandon J, Frappaz Didier, Varlet Pascale, Dufour Christelle, Beccaria Kevin, Blauwblomme Thomas, Martignetti Loredana, Di Marcotullio Lucia, Puget Stéphanie, Doz François, Bourdeaut Franck, Masliah-Planchon Julien, Gershon Timothy R, Mehlen Patrick, Ayrault Olivier

CTNI-03. REPLICATION-COMPETENT ADENOVIRUS-MEDIATED DOUBLE SUICIDE GENE THERAPY WITH FRACTIONATED STEREOTACTIC RADIOSURGERY IN PROGRESSIVE GLIOBLASTOMA: A PHASE 1 TRIAL

CTNI-03. 复制型腺病毒介导的双重自杀基因疗法联合分次立体定向放射外科手术治疗进展性胶质母细胞瘤:一项 I 期试验

Seth, Atul; Aggarwal, Vivek; Gershon, Timothy R; Hirbe, Angela C; Shuhaiber, Hans H; Viskochil, David; Sidhu, Alpa; Bielamowicz, Kevin J; Nickerson, Molly; Lokku, Armend; Weber, Michael D; Weintraub, Lauren; Hajjar, Fouad M; Babovic-Vuksanovic, Dusica; Walbert, Tobias; Lee, Ian; Snyder, James M; Shah, Mira M; Siddiqui, Salim M; Robin, Adam M; Brown, Stephen L; Movsas, Benjamin; Scarpace, Lisa; Horta, Erika Santos; Thoidingjam, Shivani; Siddiqui, Farzan; Nyati, Shyam

Noncanonical activation of GLI signaling in SOX2(+) cells drives medulloblastoma relapse

SOX2(+)细胞中GLI信号通路的非经典激活驱动髓母细胞瘤复发

Swiderska-Syn, Marzena; Mir-Pedrol, Júlia; Oles, Alexander; Schleuger, Olga; Salvador, April D; Greiner, Sean M; Seward, Cara; Yang, Fan; Babcock, Benjamin R; Shen, Chen; Wynn, Daniel T; Sanchez-Mejias, Avencia; Gershon, Timothy R; Martin, Vanesa; McCrea, Heather J; Lindsey, Kathryn G; Krieg, Carsten; Rodriguez-Blanco, Jezabel

Poly(2-oxazoline) nanoparticle delivery enhances the therapeutic potential of vismodegib for medulloblastoma by improving CNS pharmacokinetics and reducing systemic toxicity

聚(2-噁唑啉)纳米颗粒递送通过改善中枢神经系统药代动力学和降低全身毒性,增强了维莫德吉治疗髓母细胞瘤的潜力。

Hwang, Duhyeong; Dismuke, Taylor; Tikunov, Andrey; Rosen, Elias P; Kagel, John R; Ramsey, Jacob D; Lim, Chaemin; Zamboni, William; Kabanov, Alexander V; Gershon, Timothy R; Sokolsky-Papkov PhD, Marina

Content and Performance of the MiniMUGA Genotyping Array: A New Tool To Improve Rigor and Reproducibility in Mouse Research

MiniMUGA基因分型芯片的内容和性能:提高小鼠研究严谨性和可重复性的新工具

Sigmon, John Sebastian; Blanchard, Matthew W; Baric, Ralph S; Bell, Timothy A; Brennan, Jennifer; Brockmann, Gudrun A; Burks, A Wesley; Calabrese, J Mauro; Caron, Kathleen M; Cheney, Richard E; Ciavatta, Dominic; Conlon, Frank; Darr, David B; Faber, James; Franklin, Craig; Gershon, Timothy R; Gralinski, Lisa; Gu, Bin; Gaines, Christiann H; Hagan, Robert S; Heimsath, Ernest G; Heise, Mark T; Hock, Pablo; Ideraabdullah, Folami; Jennette, J Charles; Kafri, Tal; Kashfeen, Anwica; Kulis, Mike; Kumar, Vivek; Linnertz, Colton; Livraghi-Butrico, Alessandra; Lloyd, K C Kent; Lutz, Cathleen; Lynch, Rachel M; Magnuson, Terry; Matsushima, Glenn K; McMullan, Rachel; Miller, Darla R; Mohlke, Karen L; Moy, Sheryl S; Murphy, Caroline E Y; Najarian, Maya; O'Brien, Lori; Palmer, Abraham A; Philpot, Benjamin D; Randell, Scott H; Reinholdt, Laura; Ren, Yuyu; Rockwood, Steve; Rogala, Allison R; Saraswatula, Avani; Sassetti, Christopher M; Schisler, Jonathan C; Schoenrock, Sarah A; Shaw, Ginger D; Shorter, John R; Smith, Clare M; St Pierre, Celine L; Tarantino, Lisa M; Threadgill, David W; Valdar, William; Vilen, Barbara J; Wardwell, Keegan; Whitmire, Jason K; Williams, Lucy; Zylka, Mark J; Ferris, Martin T; McMillan, Leonard; Manuel de Villena, Fernando Pardo

Projected t-SNE for batch correction

用于批次校正的预测 t-SNE

Aliverti, Emanuele; Tilson, Jeffrey L; Filer, Dayne L; Babcock, Benjamin; Colaneri, Alejandro; Ocasio, Jennifer; Gershon, Timothy R; Wilhelmsen, Kirk C; Dunson, David B