Programmable siRNA pro-drugs that activate RNAi activity in response to specific cellular RNA biomarkers
可编程的 siRNA 前体药物,可响应特定的细胞 RNA 生物标志物激活 RNAi 活性
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2021.12.039
Si-Ping Han, Lisa Scherer, Matt Gethers, Ane M Salvador, Marwa Ben Haj Salah, Rebecca Mancusi, Sahil Sagar, Robin Hu, Julia DeRogatis, Ya-Huei Kuo, Guido Marcucci, Saumya Das, John J Rossi, William A Goddard 3rd