日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

New Validated Staging System for Light Chain (AL) Amyloidosis With Stage IIIC Defining Ultra-Poor Risk: AL International Staging System

新的经验证的轻链(AL)淀粉样变性分期系统,其中IIIC期定义了超高危:AL国际分期系统

Khwaja, Jahanzaib; Kirkwood, Amy A; Milani, Paolo; Yohannan, Binoy; Theodorakakou, Foteini; Weverling, Flores; Di Simone, Valeria; Ravichandran, Sriram; Kumar, Shaji; Petropoulos, Ioannis; Mussinelli, Roberta; Cohen, Oliver; Oerlemans, Marish I F J; Muchtar, Eli; Stamatelopoulos, Kimon; Lachmann, Helen J; Gillmore, Julian D; Briasoulis, Alexandros; Gertz, Morie; Whelan, Carol; Venneri, Lucia; Fontana, Marianna; Mahmood, Shameem; Schwotzer, Rahel; Minnema, Monique C; Dispenzieri, Angela; Palladini, Giovanni; Kastritis, Efstathios; Wechalekar, Ashutosh

Transthyretin amyloid cardiomyopathy: from cause to novel treatments

转甲状腺素蛋白淀粉样变性心肌病:从病因到新型疗法

Fontana, Marianna; Aimo, Alberto; Emdin, Michele; Porcari, Aldostefano; Solomon, Scott D; Hawkins, Philip N; Gillmore, Julian D

Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension

Acoramidis治疗野生型和变异型转甲状腺素蛋白淀粉样变性心肌病的疗效:来自ATTRibute-CM及其开放标签扩展研究的结果

Alexander, Kevin M; Davis, Margot K; Akinboboye, Olakunle; Berk, John; Bhatt, Kunal; Cappelli, Francesco; Cuddy, Sarah A M; Fontana, Marianna; Garcia-Pavia, Pablo; Gillmore, Julian D; Griffin, Jan M; Grodin, Justin L; Judge, Daniel P; Khouri, Michel G; Lam, Kaitlyn; Masri, Ahmad; Maurer, Mathew S; Obici, Laura; Ruberg, Frederick L; Sarswat, Nitasha; Shah, Keyur; Soman, Prem; Stern, Lily; Wright, Richard; Xiong, Kuangnan; Cao, Xiaofan; Lystig, Ted; Tamby, Jean-François; Castaño, Adam; Katz, Leonid; Sinha, Uma; Fox, Jonathan C; Solomon, Scott D; Grogan, Martha

Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial

Acoramidis治疗转甲状腺素蛋白淀粉样变性心肌病的长期疗效:ATTRibute-CM随机临床试验的开放标签扩展研究

Soman, Prem; Cuddy, Sarah A M; Gillmore, Julian D; Sarswat, Nitasha; Judge, Daniel P; Cappelli, Francesco; Stern, Lily K; Wright, Richard; Akinboboye, Olakunle; Obici, Laura; Bhatt, Kunal; Xiong, Kuangnan; Castaño, Adam; Chen, Chris; Falvey, Heather; Pecoraro, Maria Lucia; Tamby, Jean-François; Sinha, Uma; Fox, Jonathan C; Shah, Keyur; Grodin, Justin L; Ambardekar, Amrut V; Alexander, Kevin M; Khouri, Michel G; Cheng, Richard K

Current Standards and Perspectives in Proteomics for Cardiac Amyloidosis

心脏淀粉样变性蛋白质组学的当前标准和展望

Greco, Francesco; McPhail, Ellen; Canetti, Diana; Masri, Ahmad; Ferrari Chen, Yu Fu; Menichetti, Luca; Aimo, Alberto; Franzini, Maria; Ciccone, Lidia; Pucci, Angela; Castiglione, Vincenzo; Limongelli, Giuseppe; Merlo, Marco; Sinagra, Gianfranco; Basso, Cristina; Fontana, Marianna; Gillmore, Julian D; McDonnell, Liam Andrew; Emdin, Michele; Merlini, Giampaolo; Vergaro, Giuseppe

Host response to bacteria induces a shift towards the enteroendocrine cell lineage in the murine enteroid model.

在小鼠肠类器官模型中,宿主对细菌的反应会诱导向肠内分泌细胞谱系的转变。

Nissan Marry, Ranger Adrienne, Meade Justin J, Gillmore Victoria, Lehn Maija E, Cabral-Fernandes Liliane, Tsang Derek K L, Gray-Owen Scott D, Philpott Dana J, Girardin Stephen E

Acoramidis in transthyretin amyloid cardiomyopathy: expanding evidence from ATTRibute-CM

Acoramidis 在转甲状腺素蛋白淀粉样变性心肌病中的应用:来自 ATTRibute-CM 的更多证据

Sarswat, Nitasha; Ambardekar, Amrut V; Alexander, Kevin M; Cuddy, Sarah Am; Stern, Lily; Poulsen, Steen Hvitfeldt; Tschöpe, Carsten; Sekijima, Yoshiki; Sheikh, Farooq H; Griffin, Jan M; Judge, Daniel P; Gillmore, Julian; Masri, Ahmad

Transthyretin amyloid cardiomyopathy: natural history and treatment response assessed by cardiovascular magnetic resonance

转甲状腺素蛋白淀粉样变性心肌病:心血管磁共振评估其自然病程和治疗反应

Patel, Rishi K; Ioannou, Adam; Sheikh, Awais; Razvi, Yousuf; Mansell, Josephine; Martinez-Naharro, Ana; Knight, Daniel; Kotecha, Tushar; Porcari, Aldostefano; Chacko, Liza; Brown, James; Manisty, Charlotte; Moon, James C; Lachmann, Helen J; Wechalekar, Ashutosh; Whelan, Carol; Venneri, Lucia; Kellman, Peter; Hawkins, Philip N; Gillmore, Julian D; Fontana, Marianna

Kidney Outcomes in Transthyretin Amyloid Cardiomyopathy

转甲状腺素蛋白淀粉样变性心肌病患者的肾脏结局

Ioannou, Adam; Razvi, Yousuf; Porcari, Aldostefano; Rauf, Muhammad U; Martinez-Naharro, Ana; Venneri, Lucia; Kazi, Salsabeel; Pasyar, Ali; Luxhøj, Carina M; Petrie, Aviva; Moody, William; Steeds, Richard P; Sperry, Brett W; Witteles, Ronald M; Whelan, Carol; Wechalekar, Ashutosh; Lachmann, Helen; Hawkins, Philip N; Solomon, Scott D; Gillmore, Julian D; Fontana, Marianna

Clinical Phenotype and Prognosis of Asymptomatic Patients With Transthyretin Cardiac Amyloid Infiltration

无症状转甲状腺素蛋白淀粉样蛋白心脏浸润患者的临床表型和预后

Porcari, Aldostefano; Razvi, Yousuf; Cappelli, Francesco; Nitsche, Christian; Serenelli, Matteo; Longhi, Simone; Sinigiani, Giulio; Cipriani, Alberto; Aimo, Alberto; Tomasoni, Daniela; Zampieri, Mattia; Cantone, Anna; Allegro, Valentina; Vergaro, Giuseppe; Masri, Ahmad; Urey, Marcus; Ioannou, Adam; Petrie, Aviva; Noory, Navid; Gustafsson, Finn; Poledniczek, Michael; Emdin, Michele; Metra, Marco; Sinagra, Gianfranco; Martinez-Naharro, Ana; Wechalekar, Ashutosh D; Lachman, Helen; Whelan, Carol; Hawkins, Philip N; Solomon, Scott D; Gillmore, Julian D; Fontana, Marianna