日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Obefazimod in patients with moderate-to-severely active ulcerative colitis: efficacy and safety analysis from the 96-week open-label maintenance phase 2b study

奥贝法齐莫德治疗中重度活动性溃疡性结肠炎患者的疗效和安全性分析:一项为期 96 周的开放标签维持期 2b 研究

Vermeire, Severine; Nitcheu, Josianne; Gineste, Paul; Flatres, Aurélien; Santo, Julien; Scherrer, Didier; Peyrin-Biroulet, Laurent; Dulai, Parambir S; Danese, Silvio; Dubinsky, Marla; Tilg, Herbert; Siegmund, Britta; Hisamatsu, Tadakazu; Shan, Kejia; Rabbat, Christopher J; Sands, Bruce E

Myosin inhibition partially rescues the myofiber proteome in X-linked myotubular myopathy

肌球蛋白抑制可部分挽救X连锁肌管性肌病中的肌纤维蛋白质组。

Gerlach Melhedegaard, Elise; Rostedt, Fanny; Gineste, Charlotte; Seaborne, Robert Ae; Dugdale, Hannah F; Belhac, Vladimir; Zanoteli, Edmar; Lawlor, Michael W; Mack, David L; Wallgren-Pettersson, Carina; Hessel, Anthony L; Jungbluth, Heinz; Laporte, Jocelyn; Saito, Yoshihiko; Nishino, Ichizo; Ochala, Julien; Laitila, Jenni

Integrative Multi-Omics and Network Analyses Reveal Pathogenic and Protective Pathways in Centronuclear Myopathies

整合多组学和网络分析揭示中心核肌病中的致病和保护通路

Simon, Alix; Gineste, Charlotte; Reiss, David; Thompson, Julie D; Laporte, Jocelyn

Tamoxifen treatment fails to improve muscle dysfunction in a model of recessive RYR1-linked centronuclear myopathy

在隐性RYR1相关中心核肌病模型中,他莫昔芬治疗未能改善肌肉功能障碍。

Gineste, Charlotte; Reiss, David; Laporte, Jocelyn

Dietary pro-oxidant therapy by a vitamin K precursor targets PI 3-kinase VPS34 function.

通过维生素 K 前体进行膳食促氧化疗法,可靶向 PI 3-激酶 VPS34 的功能

Swamynathan Manojit M, Kuang Shan, Watrud Kaitlin E, Doherty Mary R, Gineste Charlotte, Mathew Grinu, Gong Grace Q, Cox Hilary, Cheng Eileen, Reiss David, Kendall Jude, Ghosh Diya, Reczek Colleen R, Zhao Xiang, Herzka Tali, Špokaitė Saulė, Dessus Antoine N, Kim Seung Tea, Klingbeil Olaf, Liu Juan, Nowak Dawid G, Alsudani Habeeb, Wee Tse-Luen, Park Youngkyu, Minicozzi Francesca, Rivera Keith, Almeida Ana S, Chang Kenneth, Chakrabarty Ram P, Wilkinson John E, Gimotty Phyllis A, Diermeier Sarah D, Egeblad Mikala, Vakoc Christopher R, Locasale Jason W, Chandel Navdeep S, Janowitz Tobias, Hicks James B, Wigler Michael, Pappin Darryl J, Williams Roger L, Cifani Paolo, Tuveson David A, Laporte Jocelyn, Trotman Lloyd C

Unraveling complexity: morbidity factors in elderly kidney transplant recipients

揭开复杂性:老年肾移植受者的发病因素

Gineste, Alexandra; Malvezzi, Paolo; Jouve, Thomas; Millet, Claire; Rostaing, Lionel; Noble, Johan

Tirasemtiv enhances submaximal muscle tension in an Acta1:p.Asp286Gly mouse model of nemaline myopathy

Tirasemtiv 可增强 Acta1:p.Asp286Gly 小鼠杆状体肌病模型中的亚最大肌肉张力

Ricardo A Galli, Tamara C Borsboom, Charlotte Gineste, Lorenza Brocca, Maira Rossi, Darren T Hwee, Fady I Malik, Roberto Bottinelli, Julien Gondin, Maria-Antonietta Pellegrino, Josine M de Winter, Coen A C Ottenheijm

Tamoxifen improves muscle structure and function of Bin1- and Dnm2-related centronuclear myopathies

他莫昔芬改善 Bin1 和 Dnm2 相关中心核肌病的肌肉结构和功能

Charlotte Gineste, Alix Simon, Marie Braun, David Reiss, Jocelyn Laporte

SERPIN-Derived Small Peptide (SP16) as a Potential Therapeutic Agent against HIV-Induced Inflammatory Molecules and Viral Replication in Cells of the Central Nervous System

SERPIN 衍生的小肽 (SP16) 可作为抗 HIV 诱发的中枢神经系统细胞炎症分子和病毒复制的潜在治疗剂

Yemmy Soler, Myosotys Rodriguez, Dana Austin, Cyrille Gineste, Cohava Gelber, Nazira El-Hage

ABX464 (obefazimod) for patients with COVID-19 at risk for severe disease: miR-AGE, a randomized, double-blind placebo-controlled trial

ABX464(奥贝法齐莫德)用于有重症风险的 COVID-19 患者:miR-AGE,一项随机、双盲、安慰剂对照试验

Giavina-Bianchi, Pedro; Cua, Eric; Risso, Karine; Mondain, Véronique; Vissian, Anaïs; Joie, Cécile; Pouletty, Philippe; Gineste, Paul; Ehrlich, Hartmut J; Kalil, Jorge