Gene Therapy for Parkinson's Disease: Preclinical Evaluation of Optimally Configured TH:CH1 Fusion for Maximal Dopamine Synthesis
帕金森病基因治疗:优化配置的TH:CH1融合基因实现最大多巴胺合成的临床前评估
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2019.07.002
Badin, Romina Aron; Binley, Katie; Van Camp, Nadja; Jan, Caroline; Gourlay, Jeanne; Robert, Camille; Gipchtein, Pauline; Fayard, Audrey; Stewart, Hannah; Ralph, G Scott; Lad, Yatish; Kelleher, Michelle; Loader, Julie; Hosomi, Koichi; Palfi, Stéphane; Mitrophanous, Kyriacos A; Hantraye, Philippe