TuberOus SClerosis registry to increase disease Awareness (TOSCA) - baseline data on 2093 patients
结节性硬化症登记研究旨在提高公众对疾病的认识(TOSCA)——2093名患者的基线数据
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-016-0553-5
Kingswood, John C; d'Augères, Guillaume B; Belousova, Elena; Ferreira, José C; Carter, Tom; Castellana, Ramon; Cottin, Vincent; Curatolo, Paolo; Dahlin, Maria; de Vries, Petrus J; Feucht, Martha; Fladrowski, Carla; Gislimberti, Gabriella; Hertzberg, Christoph; Jozwiak, Sergiusz; Lawson, John A; Macaya, Alfons; Nabbout, Rima; O'Callaghan, Finbar; Benedik, Mirjana P; Qin, Jiong; Marques, Ruben; Sander, Valentin; Sauter, Matthias; Takahashi, Yukitoshi; Touraine, Renaud; Youroukos, Sotiris; Zonnenberg, Bernard; Jansen, Anna C