Effective delivery of large genes to the retina by dual AAV vectors
通过双 AAV 载体有效将大基因递送至视网膜
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.1002/emmm.201302948
Ivana Trapani, Pasqualina Colella, Andrea Sommella, Carolina Iodice, Giulia Cesi, Sonia de Simone, Elena Marrocco, Settimio Rossi, Massimo Giunti, Arpad Palfi, Gwyneth J Farrar, Roman Polishchuk, Alberto Auricchio