日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

RNA editing for the treatment of alpha-1 antitrypsin deficiency.

RNA 编辑用于治疗 α-1 抗胰蛋白酶缺乏症。

Monian Prashant, Shivalila Chikdu, Lu Genliang, Bowman Keith, Briem Stearne, Bylsma Marissa, Byrne Michael, Cannon Megan, Chatterjee Arindom, Dallaire Morgan, Desai Jigar, Dufresne Jason, Faraone Alyse, Favaloro Frank, Friend Stephen, Ghosh Anamitra, Godfrey Jack, Hernandez Nidia, Huth Olivia, Iwamoto Naoki, Kawamoto Tomomi, Lamattina Anthony, Lemaitre Muriel, Lindsey Amber, Liu Fangjun, Looby Richard, Luu Khoa, McGlynn Andrew, Metterville Jake, Paik Ik-Hyeon, Pan Qianli, Patil Saurabh, Pu Tom, Purcell-Estabrook Erin, Ranade Ashwini, Rheinhardt Jeanette, Rossi Jeff, Shimizu Mamoru, Singh Kuldeep, Standley Stephany, Thomas Carina, Tripathi Snehlata, Yang Hailin, Yordanoff Ryan, Yin Yuan, Yu Hui, Narayanan PadmaKumar, Kandasamy Pachamuthu, Giangrande Paloma H, Vargeese Chandra

Calcium channel-coupled transcription factors facilitate direct nuclear signaling.

钙通道偶联转录因子促进直接的核信号传导

Rao Eshaan R, Thaxton Tyler, Gama Eric, Godfrey Jack, Wei Cenfu, Lin Qiaoshan, Li Yan, Pastor Daniel Parviz Hejazi, Hansel Christian, Du Xiaofei, Gomez Christopher M

Quantitative Measurement of Cytosolic and Nuclear Penetration of Oligonucleotide Therapeutics

寡核苷酸疗法胞质和核渗透的定量测定

Deprey, Kirsten; Batistatou, Nefeli; Debets, Marjoke F; Godfrey, Jack; VanderWall, Kirstin B; Miles, Rebecca R; Shehaj, Livia; Guo, Jiaxing; Andreucci, Amy; Kandasamy, Pachamuthu; Lu, Genliang; Shimizu, Mamoru; Vargeese, Chandra; Kritzer, Joshua A