Outcomes of early-treated infants with spinal muscular atrophy: A multicenter, retrospective cohort study
早期治疗脊髓性肌萎缩症患儿的预后:一项多中心回顾性队列研究
期刊:Muscle & Nerve
影响因子:3.1
doi:10.1002/mus.28267
Goedeker, Natalie L; Rogers, Amanda; Fisher, Mark; Arya, Kapil; Brandsema, John F; Farah, Hiba; Farrar, Michelle A; Felker, Marcia V; Gibbons, Melissa; Hamid, Omer Abdul; Harmelink, Matthew; Herbert, Karen; Kichula, Elizabeth; King, Kiana; Lakhotia, Arpita; Lee, Bo Hoon; Kuntz, Nancy L; Parsons, Julie; Rehborg, Rebecca; Veerapaniyan, Aravindhan; Zaidman, Craig M