日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Design of efficacious somatic cell genome editing strategies for recessive and polygenic diseases

针对隐性和多基因疾病的有效体细胞基因组编辑策略的设计

Jared Carlson-Stevermer, Amritava Das, Amr A Abdeen, David Fiflis, Benjamin I Grindel, Shivani Saxena, Tugce Akcan, Tausif Alam, Heidi Kletzien, Lucille Kohlenberg, Madelyn Goedland, Micah J Dombroe, Krishanu Saha

iPSC-derived hepatocytes generated from NASH donors provide a valuable platform for disease modeling and drug discovery

由非酒精性脂肪性肝炎(NASH)患者来源的诱导多能干细胞(iPSC)衍生的肝细胞,为疾病建模和药物研发提供了一个宝贵的平台。

Igor Gurevich ,Sarah A Burton ,Christie Munn ,Makiko Ohshima ,Madelyn E Goedland ,Katherine Czysz ,Deepika Rajesh

Assembly of CRISPR ribonucleoproteins with biotinylated oligonucleotides via an RNA aptamer for precise gene editing

通过 RNA 适体组装 CRISPR 核糖核蛋白与生物素化寡核苷酸,实现精准基因编辑

Jared Carlson-Stevermer, Amr A Abdeen, Lucille Kohlenberg, Madelyn Goedland, Kaivalya Molugu, Meng Lou, Krishanu Saha

High-Content Analysis of CRISPR-Cas9 Gene-Edited Human Embryonic Stem Cells

利用CRISPR-Cas9基因编辑技术对人类胚胎干细胞进行高内涵分析

Carlson-Stevermer, Jared; Goedland, Madelyn; Steyer, Benjamin; Movaghar, Arezoo; Lou, Meng; Kohlenberg, Lucille; Prestil, Ryan; Saha, Krishanu