日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

作者更正:鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

DIS3 licenses B cells for plasma cell differentiation in humans

DIS3 赋予 B 细胞在人体内分化为浆细胞的潜能

Miglierina, Emma; Bouder, Julien; Ordanoska, Delfina; Pineau, Maïwenn; Léonard, Simon; Schavgoulidze, Anaïs; Quéré, Gwenaëlle; Le Goff, Maeva; Bouchet, Maé; Genebrier, Steve Alexandre; Trinca, Samuel Bastos Serra; Deleurme, Laurent; Monvoisin, Céline; Derrier, Laure; Dumontet, Charles; Delpy, Laurent; Moreaux, Jérôme; Corre, Jill; Cogné, Michel; Laffleur, Brice

The 3D architecture of the ctenophore aboral organ and the evolution of complex integrative centers in animals

栉水母反口器官的三维结构及动物复杂整合中心的演化

Ferraioli, Anna; Digel, Leonid; Sturm, Daniela; Colgren, Jeffrey; Le Goff, Carine; Jan, Alexandre; Soto-Angel, Joan J; Naumann, Benjamin; Kittelmann, Maike; Burkhardt, Pawel

Monocyte-Derived Macrophages-Synovial Fibroblasts Crosstalk Unravels Oncostatin Signaling Network as a Driver of Synovitis in Osteoarthritis

单核细胞来源的巨噬细胞-滑膜成纤维细胞相互作用揭示了抑癌素信号网络作为骨关节炎滑膜炎驱动因素的作用

Laouteouet, Damien; Bortolotti, Olivier; Marineche, Léa; Hannemann, Nicole; Chambon, Manon; Glasson, Yaël; Dumé, Anne-Sophie; De Lima, Julien; Fournial, Maud; Touchet, Dylan; Séverac, Dany; Leccia, Felicia; Duperray, Christophe; Michaud, Henri-Alexandre; Djouad, Farida; Le Goff, Benoît; Blanchard, Frédéric; Apparailly, Florence; Courties, Gabriel

Lifelong Evolution of Autoreactive Plasma Cell Numbers, Affinity, and Anatomic Location in Arthritic K/BxN Mice

关节炎K/BxN小鼠自身反应性浆细胞数量、亲和力和解剖位置的终生演变

Vanhoucke, Thibault; Castrillon, Carlos; Richard-Le Goff, Odile; Perima, Angga; Broketa, Matteo; Griffiths, Andrew D; England, Patrick; Huetz, François; Bruhns, Pierre

Perspectives on Clinical Champions Implementing Hospital-Based Opioid Treatment in US Hospitals

美国医院中临床领军人物实施院内阿片类药物治疗的视角

Peng, Linda; Goff, Amelia; Patten, Alisa; Bazzi, Angela R; King, Carla; Siegler, Tracy; Weinstein, Zoe; Shearer, Riley; Hagedorn, Hildi; Oot, Emily; Bart, Gavin; Ghitza, Udi E; Englander, Honora

Return of genome-informed risk-assessment results for common conditions to 23,840 adults and children: An eMERGE network study

向 23,840 名成人和儿童反馈常见疾病的基因组信息风险评估结果:一项 eMERGE 网络研究

Lawson, Lucinda P; Prows, Cynthia A; Cortopassi, Josh; Davis, Kyle W; Head, Madilyn; Martin, Lisa J; Perez, Emma F; Sobowale, Agboade; Abul-Husn, Noura S; Bangash, Hana; Bland, Harris T; Bonini, Katherine E; Chisholm, Rex L; Chung, Wendy K; Cimino, James J; Connolly, John J; Crosslin, David R; Freimuth, Robert R; Goff, Blake; Gordon, Adam S; Hakonarson, Hakon; Harr, Margaret H; Henricks, Emma; Hernandez, Valentina; Hoell, Christin; Holm, Ingrid A; Hripcsak, George; Karlson, Elizabeth W; Kenny, Eimear E; Khan, Atlas; Kiryluk, Krzysztof; Kottyan, Leah C; Lennon, Niall J; Limdi, Nita; Linder, Jodell E; Liu, Cong; Manolio, Teri A; Maradik, Mary A; Marathe, Priya N; Maripuri, Devi P; McNally, Elizabeth M; Murphy, Shawn N; Naderian, Mohammadreza; Namjou, Bahram; Odgis, Jacqueline A; Peterson, Josh F; Pineda-Alvarez, Daniel E; Puckelwartz, Megan; Purcell, Jasmine; Rasmussen-Torvik, Laura J; Roden, Dan M; Rosenthal, Elisabeth A; Rowley, Robb; Sabatello, Maya; Scherr, Courtney L; Shaibi, Gabriel Q; Sharp, Richard R; Smoller, Jordan W; Sterling, Rene; Suckiel, Sabrina A; Terek, Shannon; Ting, Yi-Lee; Velez Edwards, Digna R; Walunas, Theresa L; Wei, Wei-Qi; Weng, Chunhua; Wiesner, Georgia L; Xian, Su; Jarvik, Gail P; Kullo, Iftikhar

Arsenic disrupts autophagosome-lysosome fusion in a zinc dependent manner across multiple human skin and lung cells lines

砷以锌依赖的方式破坏多种人类皮肤和肺细胞系中的自噬体-溶酶体融合。

Goff, Rachel V; Elmoustapha, Sidimohamed; Thomas, Shelia D; Banerjee, Mayukh

Regulation of HDL dysfunctionality by phosphatidylethanolamine links poly-unsaturated fatty acids with atherosclerotic cardiovascular diseases

磷脂酰乙醇胺对高密度脂蛋白功能障碍的调节作用将多不饱和脂肪酸与动脉粥样硬化性心血管疾病联系起来

Taradeh, Malik; Hardy, Lise M; Dahik, Veronica D; Lhomme, Marie; Wang, Hua; Reydellet, Canelle; Materne, Clément; Kc, Pukar; Bun, Eric; Clemessy, Maud; Pais-De-Barros, Jean-Paul; Galier, Sophie; Frisdal, Eric; Durand, Hervé; Ponnaiah, Maharajah; El Khoury, Petra; Villard, Elise F; Lesnik, Philippe; Gallo, Antonio; Kappeler, Laurent; Giral, Philippe; Bruckert, Eric; Masson, David; Guerin, Maryse; Kontush, Anatol; Guillas, Isabelle; Le Goff, Wilfried