Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A
肌联蛋白剪接调控与2A型肢带型肌营养不良症钙蛋白酶3基因治疗相关的心脏毒性
期刊:Science Translational Medicine
影响因子:14.6
doi:10.1126/scitranslmed.aat6072
Lostal, William; Roudaut, Carinne; Faivre, Marine; Charton, Karine; Suel, Laurence; Bourg, Nathalie; Best, Heather; Smith, John Edward; Gohlke, Jochen; Corre, Guillaume; Li, Xidan; Elbeck, Zaher; Knöll, Ralph; Deschamps, Jack-Yves; Granzier, Henk; Richard, Isabelle