Reengineering a transmembrane protein to treat muscular dystrophy using exon skipping.
利用外显子跳跃技术改造跨膜蛋白以治疗肌肉萎缩症
期刊:Journal of Clinical Investigation
影响因子:13.6
doi:10.1172/JCI82768
Gao Quan Q, Wyatt Eugene, Goldstein Jeff A, LoPresti Peter, Castillo Lisa M, Gazda Alec, Petrossian Natalie, Earley Judy U, Hadhazy Michele, Barefield David Y, Demonbreun Alexis R, Bönnemann Carsten, Wolf Matthew, McNally Elizabeth M
