日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Building Australia's non-animal technologies ecosystem: a national cross-sector mapping and strategic insights from the non-animal technologies network (NAT-Net)

构建澳大利亚非动物技术生态系统:来自非动物技术网络(NAT-Net)的全国跨部门概览和战略见解

Waters, Shafagh A; Hill, Adam P; Pronker, Esther S; Kaiko, Gerard E; Lin, Gungun; Keely, Simon; Collie, Laura; Chrzanowski, Wojciech; Gonzalez-Cordero, Anai

Human cone photoreceptor transplantation stimulates remodeling and restores function in AIPL1 model of end-stage Leber congenital amaurosis

人类视锥细胞光感受器移植可刺激AIPL1终末期Leber先天性黑蒙模型中的重塑并恢复其功能

Procyk, Christopher A; Melati, Anna; Ribeiro, Joana; Liu, Jingshu; Branch, Matthew J; Delicata, Jamie D; Tariq, Menahil; Kalarygrou, Aikaterini A; Kapadia, Jessica; Khorsani, Majid Moshtagh; West, Emma L; Smith, Alexander J; Gonzalez-Cordero, Anai; Ali, Robin R; Pearson, Rachael A

Connecting cilium, stress response, and proteostasis abnormalities inform variant and therapy assessment in RPGRIP1 retinal organoids

连接纤毛、应激反应和蛋白质稳态异常有助于评估RPGRIP1视网膜类器官中的变异和治疗效果

Loi, To Ha; Cheng, Anson; Kim, Hani Jieun; Fernando, Milan; Nash, Benjamin M; Aryamanesh, Nader; Grigg, John R; Yang, Pengyi; Gonzalez-Cordero, Anai; Jamieson, Robyn V

Riboflavin transporter deficiency: AAV9-SLC52A2 gene therapy as a new therapeutic strategy.

核黄素转运蛋白缺乏症:AAV9-SLC52A2 基因治疗作为一种新的治疗策略

Mei Cecilia, Magliocca Valentina, Chen Xin, Massey Keith, Gonzalez-Cordero Anai, Gray Steven J, Tartaglia Marco, Bertini Enrico Silvio, Corti Stefania, Compagnucci Claudia

Australian research priorities for inherited retinal diseases: a James Lind Alliance priority setting partnership

澳大利亚遗传性视网膜疾病研究重点:詹姆斯·林德联盟优先事项设定伙伴关系

Robertson, Eden G; Hetherington, Kate; Prain, Meredith; Ma, Alan; Ayton, Lauren N; Jamieson, Robyn V; Shepard, Emily; Boyd, Leighton; Hall, Julia; Boyd, Rosemary; Karandrews, Sally; Feller, Hollie; Simunovic, Matthew P; Grigg, John R; Yamamoto, Kanae; Wakefield, Claire E; Gonzalez-Cordero, Anai

Dismantling barriers to research and clinical care for individuals with a vision impairment

消除视力障碍人士在研究和临床护理方面的障碍

Robertson, Eden G; Hetherington, Kate; Prain, Meredith; Hall, Julia; Boyd Am, Leighton; Boyd Oam, Rosemary; Shepard, Emily; Feller, Hollie; Karandrews, Sally; O'Hare, Fleur; Yamamoto, Kanae; Simunovic, Matthew P; Jamieson, Robyn V; Ma, Alan; Ayton Am, Lauren; Gonzalez-Cordero, Anai

Refate identifies chemical compounds to target trans-regulatory networks for cellular conversion.

Refate 可识别靶向细胞转化调控网络的化学化合物

Xiao Di, Sahadevan Sonu, Mangala Melissa M, Kim Hani Jieun, Fredericks Anna, Huang Hao, Jothi Raja, Tam Patrick, Gonzalez-Cordero Anai, Zyner Katherine G, Yang Pengyi

Characterization of RNA editing and gene therapy with a compact CRISPR-Cas13 in the retina

利用紧凑型 CRISPR-Cas13 在视网膜中进行 RNA 编辑和基因治疗的特性研究

Kumar, Satheesh; Hsiao, Yi-Wen; Wong, Vickie H Y; Aubin, Deborah; Wang, Jiang-Hui; Lisowski, Leszek; Rakoczy, Elizabeth P; Li, Fan; Alarcon-Martinez, Luis; Gonzalez-Cordero, Anai; Bui, Bang V; Liu, Guei-Sheung

Antioxidant and lipid supplementation improve the development of photoreceptor outer segments in pluripotent stem cell-derived retinal organoids

抗氧化剂和脂质补充剂可改善多能干细胞衍生的视网膜类器官中感光细胞外节的发育。

West, Emma L; Majumder, Paromita; Naeem, Arifa; Fernando, Milan; O'Hara-Wright, Michelle; Lanning, Emily; Kloc, Magdalena; Ribeiro, Joana; Ovando-Roche, Patrick; Shum, Ian O; Jumbu, Neeraj; Sampson, Robert; Hayes, Matt; Bainbridge, James W B; Georgiadis, Anastasios; Smith, Alexander J; Gonzalez-Cordero, Anai; Ali, Robin R

Differentiation of brain and retinal organoids from confluent cultures of pluripotent stem cells connected by nerve-like axonal projections of optic origin

由视神经来源的多能干细胞融合培养物分化而来,这些干细胞通过神经样轴突投射相互连接,最终形成脑和视网膜类器官。

Fernando, Milan; Lee, Scott; Wark, Jesse R; Xiao, Di; Lim, Benjamin Y; O'Hara-Wright, Michelle; Kim, Hani J; Smith, Grady C; Wong, Ted; Teber, Erdahl T; Ali, Robin R; Yang, Pengyi; Graham, Mark E; Gonzalez-Cordero, Anai