日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lonafarnib Clinical Trials Demonstrate Uncoupling of the Muscle-Bone Unit in Hutchinson-Gilford Progeria Syndrome

洛那法尼临床试验表明,在哈钦森-吉尔福德早衰症中,肌肉-骨骼单元发生解耦联

Kreienkamp, Raymond J; Gordon, Leslie B; Ehrbar, Rachel; Pendleton, Alicia; Schiferl, Daniel J; Lyass, Asya; Kleinman, Monica E; Snyder, Brian D; Gordon, Catherine M

Baricitinib and Lonafarnib Synergistically Target Progerin and Inflammation, Improving Lifespan and Health in Progeria Mice.

巴瑞替尼和洛那法尼协同靶向早衰蛋白和炎症,改善早衰症小鼠的寿命和健康状况

Krüger Peter, Schroll Moritz, Fenzl Felix Quirin, Hartinger Ramona, Lederer Eva-Maria, Görlach Agnes, Gordon Leslie B, Cavalcante Paola, Iacomino Nicola, Rathkolb Birgit, Pimentel Juan Antonio Aguilar, Östereicher Manuela, Spielmann Nadine, Wolf Cordula Maria, de Angelis Martin Hrabe, Djabali Karima

Abnormal Myocardial Deformation Despite Normal Ejection Fraction in Hutchinson-Gilford Progeria Syndrome

尽管射血分数正常,但哈钦森-吉尔福德早衰综合征患者仍存在异常心肌变形

Olsen, Flemming J; Biering-Sørensen, Tor; Lunze, Fatima; Hegde, Sheila M; Colan, Steven D; Ehrbar, Rachel; Massaro, Joseph; Ferraro, Alessandra M; Harrild, David M; Kleinman, Monica E; Gordon, Leslie B; Prakash, Ashwin

Intervention for critical aortic stenosis in Hutchinson-Gilford progeria syndrome

哈钦森-吉尔福德早衰综合征患者严重主动脉狭窄的介入治疗

Gordon, Leslie B; Basso, Sammy; Maestranzi, Justine; Aikawa, Elena; Clift, Cassandra L; Cammardella, Antonio Giovanni; Danesi, Tommaso Hinna; Del Nido, Pedro J; Edelman, Elazer R; Hamdy, Abeer; Hegde, Sheila M; Kleinman, Monica E; Maschietto, Nicola; Mehra, Mandeep R; Mukundan, Srinivasan; Musumeci, Francesco; Russo, Marco; Rybicki, Frank J; Shah, Pinak Bipin; Suarez, William A; Tuminelli, Kelsey; Zaleski, Katherine; Prakash, Ashwin; Gerhard-Herman, Marie

Lonafarnib improves cardiovascular function and survival in a mouse model of Hutchinson-Gilford progeria syndrome

洛那法尼可改善早衰症小鼠模型的心血管功能和生存率

Murtada, Sae-Il; Mikush, Nicole; Wang, Mo; Ren, Pengwei; Kawamura, Yuki; Ramachandra, Abhay B; Li, David S; Braddock, Demetrios T; Tellides, George; Gordon, Leslie B; Humphrey, Jay D

Clonal hematopoiesis is not prevalent in Hutchinson-Gilford progeria syndrome

克隆性造血在哈钦森-吉尔福德早衰综合征中并不常见。

Díez-Díez, Miriam; Amorós-Pérez, Marta; de la Barrera, Jorge; Vázquez, Enrique; Quintas, Ana; Pascual-Figal, Domingo A; Dopazo, Ana; Sánchez-Cabo, Fátima; Kleinman, Monica E; Gordon, Leslie B; Fuster, Valentín; Andrés, Vicente; Fuster, José J

The farnesyl transferase inhibitor (FTI) lonafarnib improves nuclear morphology in ZMPSTE24-deficient fibroblasts from patients with the progeroid disorder MAD-B

法尼基转移酶抑制剂 (FTI) lonafarnib 可改善早衰症 MAD-B 患者 ZMPSTE24 缺陷成纤维细胞的核形态。

Odinammadu, Kamsi O; Shilagardi, Khurts; Tuminelli, Kelsey; Judge, Daniel P; Gordon, Leslie B; Michaelis, Susan

Baseline Range of Motion, Strength, Motor Function, and Participation in Youth with Hutchinson-Gilford Progeria Syndrome

患有哈钦森-吉尔福德早衰症的青少年的基线活动范围、力量、运动功能和参与情况

Malloy, Julie; Berry, Emily; Correia, Annette; Fragala-Pinkham, Maria; Coucci, Sarah; Riley, Susan; Spratt, Jessica; Knight Pfaffinger, Jessica; Massaro, Joe; Ehrbar, Rachel; D'Agostino, Ralph Sr; Gurary, Ellen B; Gordon, Leslie B; Kleinman, Monica E

Skeletal maturation and long-bone growth patterns of patients with progeria: a retrospective study

早衰症患者骨骼成熟和长骨生长模式:一项回顾性研究

Tsai, Andy; Johnston, Patrick R; Gordon, Leslie B; Walters, Michele; Kleinman, Monica; Laor, Tal

Association of Lonafarnib Treatment vs No Treatment With Mortality Rate in Patients With Hutchinson-Gilford Progeria Syndrome

洛那法尼治疗与不治疗对哈钦森-吉尔福德早衰症患者死亡率的影响

Gordon, Leslie B; Shappell, Heather; Massaro, Joe; D'Agostino, Ralph B Sr; Brazier, Joan; Campbell, Susan E; Kleinman, Monica E; Kieran, Mark W