Invention of an oral medication for cardiac Fabry disease caused by RNA mis-splicing.
发明了一种用于治疗由 RNA 剪接错误引起的法布里病的口服药物
期刊:Science Advances
影响因子:12.5
doi:10.1126/sciadv.adt9695
Awaya Tomonari, Ajiro Masahiko, Kobayashi Hiroko, Sawada Teruo, Gotanda Kentoku, Noji Toshiharu, Takemoto Naohiro, Iida Kei, Saito Megumu K, Niu Dau-Ming, Hagiwara Masatoshi
