AAV-mediated transcription factor EB (TFEB) gene delivery ameliorates muscle pathology and function in the murine model of Pompe Disease
AAV 介导的转录因子 EB (TFEB) 基因传递可改善庞贝病小鼠模型中的肌肉病理和功能
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/s41598-017-15352-2
Francesca Gatto, Barbara Rossi, Antonietta Tarallo, Elena Polishchuk, Roman Polishchuk, Alessandra Carrella, Edoardo Nusco, Filomena Grazia Alvino, Francesca Iacobellis, Elvira De Leonibus, Alberto Auricchio, Graciana Diez-Roux, Andrea Ballabio, Giancarlo Parenti
