Haploidentical related donor hematopoietic stem cell transplantation with post-transplantation cyclophosphamide for DOCK8 deficiency
对于DOCK8缺陷,采用单倍体相合亲缘供者造血干细胞移植联合移植后环磷酰胺治疗。
期刊:Journal of Allergy and Clinical Immunology-In Practice
影响因子:6.6
doi:10.1016/j.jaip.2016.06.028
Freeman, Alexandra F; Shah, Nirali N; Parta, Mark; Su, Helen C; Brofferio, Alessandra; Gradus-Pizlo, Irma; Butty, Sabah; Hughes, Thomas E; Kleiner, David E; Avila, Daniele; Heller, Theo; Kong, Heidi H; Holland, Steven M; Hickstein, Dennis D